CFTR modulators and rare variants-leaping from laboratory cells to real world effectiveness?

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Bibliographic Details
Title: CFTR modulators and rare variants-leaping from laboratory cells to real world effectiveness?
Authors: Simmonds NJ; Adult Cystic Fibrosis Centre, Royal Brompton Hospital, Part of Guy's and St Thomas's NHS Foundation Trust, London, United Kingdom.; National Heart and Lung Institute, Imperial College London, London, United Kingdom., Downey DG; Wellcome-Wolfson Institute for Experimental Medicine, Queen's University Belfast, Belfast, United Kingdom.
Source: American journal of respiratory and critical care medicine [Am J Respir Crit Care Med] 2026 Feb 01; Vol. 212 (2), pp. 286-287.
Publication Type: Journal Article
Journal Info: Publisher: American Thoracic Society Country of Publication: England NLM ID: 9421642 Publication Model: Print Cited Medium: Internet ISSN: 1535-4970 (Electronic) Linking ISSN: 1073449X NLM ISO Abbreviation: Am J Respir Crit Care Med Subsets: MEDLINE; In Process
Database: MEDLINE Ultimate
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Description
ISSN:1535-4970
DOI:10.1093/ajrccm/aamaf102