Identification of a therapeutic threshold for AAV-STXBP1 gene therapy in a rodent model of STXBP1 developmental and epileptic encephalopathy.
Saved in:
| Title: | Identification of a therapeutic threshold for AAV-STXBP1 gene therapy in a rodent model of STXBP1 developmental and epileptic encephalopathy. |
|---|---|
| Authors: | Gallo NB; Biogen, Cambridge, MA 02142, USA., Annand JW; Biogen, Cambridge, MA 02142, USA., Clarner P; Biogen, Cambridge, MA 02142, USA., Harvey B; Biogen, Cambridge, MA 02142, USA., Morozova E; Biogen, Cambridge, MA 02142, USA., Ehrenfels C; Biogen, Cambridge, MA 02142, USA., Jiang T; Biogen, Cambridge, MA 02142, USA., Yuan L; Biogen, Cambridge, MA 02142, USA., Kashyap S; Biogen, Cambridge, MA 02142, USA., Lu X; Biogen, Cambridge, MA 02142, USA., Choi J; Biogen, Cambridge, MA 02142, USA., Zoll J; Biogen, Cambridge, MA 02142, USA., Nhu A; Biogen, Cambridge, MA 02142, USA., Brennecke A; Biogen, Cambridge, MA 02142, USA., Patel P; Biogen, Cambridge, MA 02142, USA., Gianni D; Biogen, Cambridge, MA 02142, USA., Guilmette E; Biogen, Cambridge, MA 02142, USA., Geisler S; Biogen, Cambridge, MA 02142, USA., Sheehy A; Biogen, Cambridge, MA 02142, USA., Ghaemi K; Biogen, Cambridge, MA 02142, USA., Benezra S; Biogen, Cambridge, MA 02142, USA., Ghoshal A; Biogen, Cambridge, MA 02142, USA., Liu Y; Biogen, Cambridge, MA 02142, USA., Carlile T; Biogen, Cambridge, MA 02142, USA., Cao S; Biogen, Cambridge, MA 02142, USA., Casey F; Biogen, Cambridge, MA 02142, USA., Koirala S; Biogen, Cambridge, MA 02142, USA., Wu S; Biogen, Cambridge, MA 02142, USA. Electronic address: sijia.wu@biogen.com. |
| Source: | Molecular therapy : the journal of the American Society of Gene Therapy [Mol Ther] 2026 Jul 01; Vol. 34 (7), pp. 3763-3782. Date of Electronic Publication: 2026 Mar 24. |
| Publication Type: | Journal Article |
| Journal Info: | Publisher: Cell Press Country of Publication: United States NLM ID: 100890581 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1525-0024 (Electronic) Linking ISSN: 15250016 NLM ISO Abbreviation: Mol Ther Subsets: MEDLINE |
| Database: | MEDLINE Ultimate |
Be the first to leave a comment!
