Long-Term Durability of Acoramidis Efficacy in Transthyretin Amyloid Cardiomyopathy: Open-Label Extension of the ATTRibute-CM Randomized Clinical Trial.

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Bibliographic Details
Title: Long-Term Durability of Acoramidis Efficacy in Transthyretin Amyloid Cardiomyopathy: Open-Label Extension of the ATTRibute-CM Randomized Clinical Trial.
Authors: Soman P; Division of Cardiology, University of Pittsburgh Medical Center, Pittsburgh, Pennsylvania., Cuddy SAM; Amyloidosis Program, Brigham and Women's Hospital, Boston, Massachusetts., Gillmore JD; National Amyloidosis Centre, Division of Medicine, Royal Free Hospital, University College London, London, United Kingdom., Sarswat N; Division of Cardiovascular Medicine, University of Chicago Medicine, Chicago, Illinois., Judge DP; Division of Cardiology, Medical University of South Carolina, Charleston., Cappelli F; Tuscan Regional Amyloidosis Centre, Careggi University Hospital, Florence, Italy.; Department of Clinical and Experimental Medicine, University of Florence, Florence, Italy., Stern LK; Department of Cardiology, Cedars-Sinai Smidt Heart Institute, Los Angeles, California., Wright R; Pacific Heart Institute, Santa Monica, California., Akinboboye O; Laurelton Heart Specialists PC, Rosedale, New York., Obici L; Amyloidosis Research and Treatment Center, Fondazione IRCCS Policlinico San Matteo, Pavia, Italy., Bhatt K; Emory Healthcare, Atlanta, Georgia., Xiong K; BridgeBio Pharma, San Francisco, California., Castaño A; BridgeBio Pharma, San Francisco, California., Chen C; BridgeBio Pharma, San Francisco, California., Falvey H; BridgeBio Pharma, San Francisco, California., Pecoraro ML; BridgeBio Pharma, San Francisco, California., Tamby JF; BridgeBio Pharma, San Francisco, California., Sinha U; BridgeBio Pharma, San Francisco, California., Fox JC; BridgeBio Pharma, San Francisco, California., Shah K; The Pauley Heart Center, Virginia Commonwealth University, Richmond., Grodin JL; Parkland Health and Hospital System, Dallas, Texas.; University of Texas Southwestern Medical Center, Dallas., Ambardekar AV; University of Colorado, Aurora., Alexander KM; Division of Cardiovascular Medicine, Department of Medicine, Stanford University School of Medicine, Stanford, California., Khouri MG; Division of Cardiovascular Medicine, Duke University School of Medicine, Durham, North Carolina., Cheng RK; University of Washington, Seattle.
Source: JAMA cardiology [JAMA Cardiol] 2026 May 01; Vol. 11 (5), pp. 446-454.
Publication Type: Journal Article; Randomized Controlled Trial; Multicenter Study
Journal Info: Publisher: American Medical Association Country of Publication: United States NLM ID: 101676033 Publication Model: Print Cited Medium: Internet ISSN: 2380-6591 (Electronic) NLM ISO Abbreviation: JAMA Cardiol Subsets: MEDLINE
Database: MEDLINE Ultimate
Description
ISSN:2380-6591
DOI:10.1001/jamacardio.2026.0819