Long-Term Durability of Acoramidis Efficacy in Transthyretin Amyloid Cardiomyopathy: Open-Label Extension of the ATTRibute-CM Randomized Clinical Trial.

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Title: Long-Term Durability of Acoramidis Efficacy in Transthyretin Amyloid Cardiomyopathy: Open-Label Extension of the ATTRibute-CM Randomized Clinical Trial.
Authors: Soman P; Division of Cardiology, University of Pittsburgh Medical Center, Pittsburgh, Pennsylvania., Cuddy SAM; Amyloidosis Program, Brigham and Women's Hospital, Boston, Massachusetts., Gillmore JD; National Amyloidosis Centre, Division of Medicine, Royal Free Hospital, University College London, London, United Kingdom., Sarswat N; Division of Cardiovascular Medicine, University of Chicago Medicine, Chicago, Illinois., Judge DP; Division of Cardiology, Medical University of South Carolina, Charleston., Cappelli F; Tuscan Regional Amyloidosis Centre, Careggi University Hospital, Florence, Italy.; Department of Clinical and Experimental Medicine, University of Florence, Florence, Italy., Stern LK; Department of Cardiology, Cedars-Sinai Smidt Heart Institute, Los Angeles, California., Wright R; Pacific Heart Institute, Santa Monica, California., Akinboboye O; Laurelton Heart Specialists PC, Rosedale, New York., Obici L; Amyloidosis Research and Treatment Center, Fondazione IRCCS Policlinico San Matteo, Pavia, Italy., Bhatt K; Emory Healthcare, Atlanta, Georgia., Xiong K; BridgeBio Pharma, San Francisco, California., Castaño A; BridgeBio Pharma, San Francisco, California., Chen C; BridgeBio Pharma, San Francisco, California., Falvey H; BridgeBio Pharma, San Francisco, California., Pecoraro ML; BridgeBio Pharma, San Francisco, California., Tamby JF; BridgeBio Pharma, San Francisco, California., Sinha U; BridgeBio Pharma, San Francisco, California., Fox JC; BridgeBio Pharma, San Francisco, California., Shah K; The Pauley Heart Center, Virginia Commonwealth University, Richmond., Grodin JL; Parkland Health and Hospital System, Dallas, Texas.; University of Texas Southwestern Medical Center, Dallas., Ambardekar AV; University of Colorado, Aurora., Alexander KM; Division of Cardiovascular Medicine, Department of Medicine, Stanford University School of Medicine, Stanford, California., Khouri MG; Division of Cardiovascular Medicine, Duke University School of Medicine, Durham, North Carolina., Cheng RK; University of Washington, Seattle.
Source: JAMA cardiology [JAMA Cardiol] 2026 May 01; Vol. 11 (5), pp. 446-454.
Publication Type: Journal Article; Randomized Controlled Trial; Multicenter Study
Journal Info: Publisher: American Medical Association Country of Publication: United States NLM ID: 101676033 Publication Model: Print Cited Medium: Internet ISSN: 2380-6591 (Electronic) NLM ISO Abbreviation: JAMA Cardiol Subsets: MEDLINE
Database: MEDLINE Ultimate
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  Data: Long-Term Durability of Acoramidis Efficacy in Transthyretin Amyloid Cardiomyopathy: Open-Label Extension of the ATTRibute-CM Randomized Clinical Trial.
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  Data: <searchLink fieldCode="AU" term="%22Soman+P%22">Soman P</searchLink>; Division of Cardiology, University of Pittsburgh Medical Center, Pittsburgh, Pennsylvania.<br /><searchLink fieldCode="AU" term="%22Cuddy+SAM%22">Cuddy SAM</searchLink>; Amyloidosis Program, Brigham and Women's Hospital, Boston, Massachusetts.<br /><searchLink fieldCode="AU" term="%22Gillmore+JD%22">Gillmore JD</searchLink>; National Amyloidosis Centre, Division of Medicine, Royal Free Hospital, University College London, London, United Kingdom.<br /><searchLink fieldCode="AU" term="%22Sarswat+N%22">Sarswat N</searchLink>; Division of Cardiovascular Medicine, University of Chicago Medicine, Chicago, Illinois.<br /><searchLink fieldCode="AU" term="%22Judge+DP%22">Judge DP</searchLink>; Division of Cardiology, Medical University of South Carolina, Charleston.<br /><searchLink fieldCode="AU" term="%22Cappelli+F%22">Cappelli F</searchLink>; Tuscan Regional Amyloidosis Centre, Careggi University Hospital, Florence, Italy.; Department of Clinical and Experimental Medicine, University of Florence, Florence, Italy.<br /><searchLink fieldCode="AU" term="%22Stern+LK%22">Stern LK</searchLink>; Department of Cardiology, Cedars-Sinai Smidt Heart Institute, Los Angeles, California.<br /><searchLink fieldCode="AU" term="%22Wright+R%22">Wright R</searchLink>; Pacific Heart Institute, Santa Monica, California.<br /><searchLink fieldCode="AU" term="%22Akinboboye+O%22">Akinboboye O</searchLink>; Laurelton Heart Specialists PC, Rosedale, New York.<br /><searchLink fieldCode="AU" term="%22Obici+L%22">Obici L</searchLink>; Amyloidosis Research and Treatment Center, Fondazione IRCCS Policlinico San Matteo, Pavia, Italy.<br /><searchLink fieldCode="AU" term="%22Bhatt+K%22">Bhatt K</searchLink>; Emory Healthcare, Atlanta, Georgia.<br /><searchLink fieldCode="AU" term="%22Xiong+K%22">Xiong K</searchLink>; BridgeBio Pharma, San Francisco, California.<br /><searchLink fieldCode="AU" term="%22Castaño+A%22">Castaño A</searchLink>; BridgeBio Pharma, San Francisco, California.<br /><searchLink fieldCode="AU" term="%22Chen+C%22">Chen C</searchLink>; BridgeBio Pharma, San Francisco, California.<br /><searchLink fieldCode="AU" term="%22Falvey+H%22">Falvey H</searchLink>; BridgeBio Pharma, San Francisco, California.<br /><searchLink fieldCode="AU" term="%22Pecoraro+ML%22">Pecoraro ML</searchLink>; BridgeBio Pharma, San Francisco, California.<br /><searchLink fieldCode="AU" term="%22Tamby+JF%22">Tamby JF</searchLink>; BridgeBio Pharma, San Francisco, California.<br /><searchLink fieldCode="AU" term="%22Sinha+U%22">Sinha U</searchLink>; BridgeBio Pharma, San Francisco, California.<br /><searchLink fieldCode="AU" term="%22Fox+JC%22">Fox JC</searchLink>; BridgeBio Pharma, San Francisco, California.<br /><searchLink fieldCode="AU" term="%22Shah+K%22">Shah K</searchLink>; The Pauley Heart Center, Virginia Commonwealth University, Richmond.<br /><searchLink fieldCode="AU" term="%22Grodin+JL%22">Grodin JL</searchLink>; Parkland Health and Hospital System, Dallas, Texas.; University of Texas Southwestern Medical Center, Dallas.<br /><searchLink fieldCode="AU" term="%22Ambardekar+AV%22">Ambardekar AV</searchLink>; University of Colorado, Aurora.<br /><searchLink fieldCode="AU" term="%22Alexander+KM%22">Alexander KM</searchLink>; Division of Cardiovascular Medicine, Department of Medicine, Stanford University School of Medicine, Stanford, California.<br /><searchLink fieldCode="AU" term="%22Khouri+MG%22">Khouri MG</searchLink>; Division of Cardiovascular Medicine, Duke University School of Medicine, Durham, North Carolina.<br /><searchLink fieldCode="AU" term="%22Cheng+RK%22">Cheng RK</searchLink>; University of Washington, Seattle.
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