Long-Term Durability of Acoramidis Efficacy in Transthyretin Amyloid Cardiomyopathy: Open-Label Extension of the ATTRibute-CM Randomized Clinical Trial.
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| Title: | Long-Term Durability of Acoramidis Efficacy in Transthyretin Amyloid Cardiomyopathy: Open-Label Extension of the ATTRibute-CM Randomized Clinical Trial. |
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| Authors: | Soman P; Division of Cardiology, University of Pittsburgh Medical Center, Pittsburgh, Pennsylvania., Cuddy SAM; Amyloidosis Program, Brigham and Women's Hospital, Boston, Massachusetts., Gillmore JD; National Amyloidosis Centre, Division of Medicine, Royal Free Hospital, University College London, London, United Kingdom., Sarswat N; Division of Cardiovascular Medicine, University of Chicago Medicine, Chicago, Illinois., Judge DP; Division of Cardiology, Medical University of South Carolina, Charleston., Cappelli F; Tuscan Regional Amyloidosis Centre, Careggi University Hospital, Florence, Italy.; Department of Clinical and Experimental Medicine, University of Florence, Florence, Italy., Stern LK; Department of Cardiology, Cedars-Sinai Smidt Heart Institute, Los Angeles, California., Wright R; Pacific Heart Institute, Santa Monica, California., Akinboboye O; Laurelton Heart Specialists PC, Rosedale, New York., Obici L; Amyloidosis Research and Treatment Center, Fondazione IRCCS Policlinico San Matteo, Pavia, Italy., Bhatt K; Emory Healthcare, Atlanta, Georgia., Xiong K; BridgeBio Pharma, San Francisco, California., Castaño A; BridgeBio Pharma, San Francisco, California., Chen C; BridgeBio Pharma, San Francisco, California., Falvey H; BridgeBio Pharma, San Francisco, California., Pecoraro ML; BridgeBio Pharma, San Francisco, California., Tamby JF; BridgeBio Pharma, San Francisco, California., Sinha U; BridgeBio Pharma, San Francisco, California., Fox JC; BridgeBio Pharma, San Francisco, California., Shah K; The Pauley Heart Center, Virginia Commonwealth University, Richmond., Grodin JL; Parkland Health and Hospital System, Dallas, Texas.; University of Texas Southwestern Medical Center, Dallas., Ambardekar AV; University of Colorado, Aurora., Alexander KM; Division of Cardiovascular Medicine, Department of Medicine, Stanford University School of Medicine, Stanford, California., Khouri MG; Division of Cardiovascular Medicine, Duke University School of Medicine, Durham, North Carolina., Cheng RK; University of Washington, Seattle. |
| Source: | JAMA cardiology [JAMA Cardiol] 2026 May 01; Vol. 11 (5), pp. 446-454. |
| Publication Type: | Journal Article; Randomized Controlled Trial; Multicenter Study |
| Journal Info: | Publisher: American Medical Association Country of Publication: United States NLM ID: 101676033 Publication Model: Print Cited Medium: Internet ISSN: 2380-6591 (Electronic) NLM ISO Abbreviation: JAMA Cardiol Subsets: MEDLINE |
| Database: | MEDLINE Ultimate |
| FullText | Text: Availability: 0 |
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| Header | DbId: mdl DbLabel: MEDLINE Ultimate An: 41911489 AccessLevel: 2 PubType: Academic Journal PubTypeId: academicJournal PreciseRelevancyScore: 0 |
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| Items | – Name: Title Label: Title Group: Ti Data: Long-Term Durability of Acoramidis Efficacy in Transthyretin Amyloid Cardiomyopathy: Open-Label Extension of the ATTRibute-CM Randomized Clinical Trial. – Name: Author Label: Authors Group: Au Data: <searchLink fieldCode="AU" term="%22Soman+P%22">Soman P</searchLink>; Division of Cardiology, University of Pittsburgh Medical Center, Pittsburgh, Pennsylvania.<br /><searchLink fieldCode="AU" term="%22Cuddy+SAM%22">Cuddy SAM</searchLink>; Amyloidosis Program, Brigham and Women's Hospital, Boston, Massachusetts.<br /><searchLink fieldCode="AU" term="%22Gillmore+JD%22">Gillmore JD</searchLink>; National Amyloidosis Centre, Division of Medicine, Royal Free Hospital, University College London, London, United Kingdom.<br /><searchLink fieldCode="AU" term="%22Sarswat+N%22">Sarswat N</searchLink>; Division of Cardiovascular Medicine, University of Chicago Medicine, Chicago, Illinois.<br /><searchLink fieldCode="AU" term="%22Judge+DP%22">Judge DP</searchLink>; Division of Cardiology, Medical University of South Carolina, Charleston.<br /><searchLink fieldCode="AU" term="%22Cappelli+F%22">Cappelli F</searchLink>; Tuscan Regional Amyloidosis Centre, Careggi University Hospital, Florence, Italy.; Department of Clinical and Experimental Medicine, University of Florence, Florence, Italy.<br /><searchLink fieldCode="AU" term="%22Stern+LK%22">Stern LK</searchLink>; Department of Cardiology, Cedars-Sinai Smidt Heart Institute, Los Angeles, California.<br /><searchLink fieldCode="AU" term="%22Wright+R%22">Wright R</searchLink>; Pacific Heart Institute, Santa Monica, California.<br /><searchLink fieldCode="AU" term="%22Akinboboye+O%22">Akinboboye O</searchLink>; Laurelton Heart Specialists PC, Rosedale, New York.<br /><searchLink fieldCode="AU" term="%22Obici+L%22">Obici L</searchLink>; Amyloidosis Research and Treatment Center, Fondazione IRCCS Policlinico San Matteo, Pavia, Italy.<br /><searchLink fieldCode="AU" term="%22Bhatt+K%22">Bhatt K</searchLink>; Emory Healthcare, Atlanta, Georgia.<br /><searchLink fieldCode="AU" term="%22Xiong+K%22">Xiong K</searchLink>; BridgeBio Pharma, San Francisco, California.<br /><searchLink fieldCode="AU" term="%22Castaño+A%22">Castaño A</searchLink>; BridgeBio Pharma, San Francisco, California.<br /><searchLink fieldCode="AU" term="%22Chen+C%22">Chen C</searchLink>; BridgeBio Pharma, San Francisco, California.<br /><searchLink fieldCode="AU" term="%22Falvey+H%22">Falvey H</searchLink>; BridgeBio Pharma, San Francisco, California.<br /><searchLink fieldCode="AU" term="%22Pecoraro+ML%22">Pecoraro ML</searchLink>; BridgeBio Pharma, San Francisco, California.<br /><searchLink fieldCode="AU" term="%22Tamby+JF%22">Tamby JF</searchLink>; BridgeBio Pharma, San Francisco, California.<br /><searchLink fieldCode="AU" term="%22Sinha+U%22">Sinha U</searchLink>; BridgeBio Pharma, San Francisco, California.<br /><searchLink fieldCode="AU" term="%22Fox+JC%22">Fox JC</searchLink>; BridgeBio Pharma, San Francisco, California.<br /><searchLink fieldCode="AU" term="%22Shah+K%22">Shah K</searchLink>; The Pauley Heart Center, Virginia Commonwealth University, Richmond.<br /><searchLink fieldCode="AU" term="%22Grodin+JL%22">Grodin JL</searchLink>; Parkland Health and Hospital System, Dallas, Texas.; University of Texas Southwestern Medical Center, Dallas.<br /><searchLink fieldCode="AU" term="%22Ambardekar+AV%22">Ambardekar AV</searchLink>; University of Colorado, Aurora.<br /><searchLink fieldCode="AU" term="%22Alexander+KM%22">Alexander KM</searchLink>; Division of Cardiovascular Medicine, Department of Medicine, Stanford University School of Medicine, Stanford, California.<br /><searchLink fieldCode="AU" term="%22Khouri+MG%22">Khouri MG</searchLink>; Division of Cardiovascular Medicine, Duke University School of Medicine, Durham, North Carolina.<br /><searchLink fieldCode="AU" term="%22Cheng+RK%22">Cheng RK</searchLink>; University of Washington, Seattle. – Name: TitleSource Label: Source Group: Src Data: <searchLink fieldCode="JN" term="%22101676033%22">JAMA cardiology</searchLink> [JAMA Cardiol] 2026 May 01; Vol. 11 (5), pp. 446-454. – Name: TypePub Label: Publication Type Group: TypPub Data: Journal Article; Randomized Controlled Trial; Multicenter Study – Name: TitleSource Label: Journal Info Group: Src Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22American+Medical+Association%22">American Medical Association </searchLink><i>Country of Publication: </i>United States <i>NLM ID: </i>101676033 <i>Publication Model: </i>Print <i>Cited Medium: </i>Internet <i>ISSN: </i>2380-6591 (Electronic) <i>NLM ISO Abbreviation: </i>JAMA Cardiol <i>Subsets: </i>MEDLINE |
| PLink | https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=mdl&AN=41911489 |
| RecordInfo | BibRecord: BibEntity: Identifiers: – Type: doi Value: 10.1001/jamacardio.2026.0819 Languages: – Code: eng Text: English PhysicalDescription: Pagination: StartPage: 446 Titles: – TitleFull: Long-Term Durability of Acoramidis Efficacy in Transthyretin Amyloid Cardiomyopathy: Open-Label Extension of the ATTRibute-CM Randomized Clinical Trial. Type: main BibRelationships: HasContributorRelationships: – PersonEntity: Name: NameFull: Soman P – PersonEntity: Name: NameFull: Cuddy SAM – PersonEntity: Name: NameFull: Gillmore JD – PersonEntity: Name: NameFull: Sarswat N – PersonEntity: Name: NameFull: Judge DP – PersonEntity: Name: NameFull: Cappelli F – PersonEntity: Name: NameFull: Stern LK – PersonEntity: Name: NameFull: Wright R – PersonEntity: Name: NameFull: Akinboboye O – PersonEntity: Name: NameFull: Obici L – PersonEntity: Name: NameFull: Bhatt K – PersonEntity: Name: NameFull: Xiong K – PersonEntity: Name: NameFull: Castaño A – PersonEntity: Name: NameFull: Chen C – PersonEntity: Name: NameFull: Falvey H – PersonEntity: Name: NameFull: Pecoraro ML – PersonEntity: Name: NameFull: Tamby JF – PersonEntity: Name: NameFull: Sinha U – PersonEntity: Name: NameFull: Fox JC – PersonEntity: Name: NameFull: Shah K – PersonEntity: Name: NameFull: Grodin JL – PersonEntity: Name: NameFull: Ambardekar AV – PersonEntity: Name: NameFull: Alexander KM – PersonEntity: Name: NameFull: Khouri MG – PersonEntity: Name: NameFull: Cheng RK IsPartOfRelationships: – BibEntity: Dates: – D: 01 M: 05 Text: 2026 May 01 Type: published Y: 2026 Identifiers: – Type: issn-electronic Value: 2380-6591 Numbering: – Type: volume Value: 11 – Type: issue Value: 5 Titles: – TitleFull: JAMA cardiology Type: main |
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