Emicizumab prophylaxis beyond clinical trials: a multicenter, prospective real-world study of pediatric hemophilia patients with and without inhibitors.
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| Title: | Emicizumab prophylaxis beyond clinical trials: a multicenter, prospective real-world study of pediatric hemophilia patients with and without inhibitors. |
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| Authors: | Sherief LM; Pediatric Hematology and Oncology Unit, Pediatric Department, Faculty of Medicine, Zagazig University, Zagazig, Egypt. lamesh25@yahoo.com., Elagamy O; Department of Pediatrics, Faculty of Medicine, Kafrelsheikh University, Kafrelsheikh, Egypt., Darwish A; Pediatric Hematology and Oncology Unit, Pediatric Department, Faculty of Medicine, Mansoura University, Mansoura, Egypt., Soliman NK; Pediatric Hematology and Oncology Unit, Pediatric Department, Faculty of Medicine, Zagazig University, Zagazig, Egypt., Elgendy MR; Pediatric Department, Mabara Health Insurance Hospital, Zagazig, Egypt., Nazim A; Pediatric Department, Mansoura Health Insurance Hospital, Mansoura, Egypt., Sobhi A; Department of Pediatrics, Faculty of Medicine, Kafrelsheikh University, Kafrelsheikh, Egypt. |
| Source: | European journal of pediatrics [Eur J Pediatr] 2026 Apr 11; Vol. 185 (5). Date of Electronic Publication: 2026 Apr 11. |
| Publication Type: | Journal Article; Multicenter Study |
| Journal Info: | Publisher: Springer Verlag Country of Publication: Germany NLM ID: 7603873 Publication Model: Electronic Cited Medium: Internet ISSN: 1432-1076 (Electronic) Linking ISSN: 03406199 NLM ISO Abbreviation: Eur J Pediatr Subsets: MEDLINE |
| Database: | MEDLINE Ultimate |
| FullText | Text: Availability: 0 |
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| Header | DbId: mdl DbLabel: MEDLINE Ultimate An: 41964698 AccessLevel: 2 PubType: Academic Journal PubTypeId: academicJournal PreciseRelevancyScore: 0 |
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| Items | – Name: Title Label: Title Group: Ti Data: Emicizumab prophylaxis beyond clinical trials: a multicenter, prospective real-world study of pediatric hemophilia patients with and without inhibitors. – Name: Author Label: Authors Group: Au Data: <searchLink fieldCode="AU" term="%22Sherief+LM%22">Sherief LM</searchLink>; Pediatric Hematology and Oncology Unit, Pediatric Department, Faculty of Medicine, Zagazig University, Zagazig, Egypt. lamesh25@yahoo.com.<br /><searchLink fieldCode="AU" term="%22Elagamy+O%22">Elagamy O</searchLink>; Department of Pediatrics, Faculty of Medicine, Kafrelsheikh University, Kafrelsheikh, Egypt.<br /><searchLink fieldCode="AU" term="%22Darwish+A%22">Darwish A</searchLink>; Pediatric Hematology and Oncology Unit, Pediatric Department, Faculty of Medicine, Mansoura University, Mansoura, Egypt.<br /><searchLink fieldCode="AU" term="%22Soliman+NK%22">Soliman NK</searchLink>; Pediatric Hematology and Oncology Unit, Pediatric Department, Faculty of Medicine, Zagazig University, Zagazig, Egypt.<br /><searchLink fieldCode="AU" term="%22Elgendy+MR%22">Elgendy MR</searchLink>; Pediatric Department, Mabara Health Insurance Hospital, Zagazig, Egypt.<br /><searchLink fieldCode="AU" term="%22Nazim+A%22">Nazim A</searchLink>; Pediatric Department, Mansoura Health Insurance Hospital, Mansoura, Egypt.<br /><searchLink fieldCode="AU" term="%22Sobhi+A%22">Sobhi A</searchLink>; Department of Pediatrics, Faculty of Medicine, Kafrelsheikh University, Kafrelsheikh, Egypt. – Name: TitleSource Label: Source Group: Src Data: <searchLink fieldCode="JN" term="%227603873%22">European journal of pediatrics</searchLink> [Eur J Pediatr] 2026 Apr 11; Vol. 185 (5). <i>Date of Electronic Publication: </i>2026 Apr 11. – Name: TypePub Label: Publication Type Group: TypPub Data: Journal Article; Multicenter Study – Name: TitleSource Label: Journal Info Group: Src Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Springer+Verlag%22">Springer Verlag </searchLink><i>Country of Publication: </i>Germany <i>NLM ID: </i>7603873 <i>Publication Model: </i>Electronic <i>Cited Medium: </i>Internet <i>ISSN: </i>1432-1076 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2203406199%22">03406199 </searchLink><i>NLM ISO Abbreviation: </i>Eur J Pediatr <i>Subsets: </i>MEDLINE |
| PLink | https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=mdl&AN=41964698 |
| RecordInfo | BibRecord: BibEntity: Identifiers: – Type: doi Value: 10.1007/s00431-026-06872-z Languages: – Code: eng Text: English Titles: – TitleFull: Emicizumab prophylaxis beyond clinical trials: a multicenter, prospective real-world study of pediatric hemophilia patients with and without inhibitors. Type: main BibRelationships: HasContributorRelationships: – PersonEntity: Name: NameFull: Sherief LM – PersonEntity: Name: NameFull: Elagamy O – PersonEntity: Name: NameFull: Darwish A – PersonEntity: Name: NameFull: Soliman NK – PersonEntity: Name: NameFull: Elgendy MR – PersonEntity: Name: NameFull: Nazim A – PersonEntity: Name: NameFull: Sobhi A IsPartOfRelationships: – BibEntity: Dates: – D: 11 M: 04 Text: 2026 Apr 11 Type: published Y: 2026 Identifiers: – Type: issn-electronic Value: 1432-1076 Numbering: – Type: volume Value: 185 – Type: issue Value: 5 Titles: – TitleFull: European journal of pediatrics Type: main |
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