Next-Generation Therapies for Genetic Diseases: The Synergy of CRISPR and Gene Therapy.

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Title: Next-Generation Therapies for Genetic Diseases: The Synergy of CRISPR and Gene Therapy.
Authors: Karwa P; Dr. D.Y. Patil Institute of Pharmaceutical Sciences and Research, Pimpri, Pune, 411018, India. pawan.karwa@dypvp.edu.in.; School of Pharmacy and Research, Dnyaan Prasad Global University, Pimpri, Pune, India. pawan.karwa@dypvp.edu.in., Kharul A; Dr. D.Y. Patil Institute of Pharmaceutical Sciences and Research, Pimpri, Pune, 411018, India.; School of Pharmacy and Research, Dnyaan Prasad Global University, Pimpri, Pune, India., Parekar V; Dr. D.Y. Patil Institute of Pharmaceutical Sciences and Research, Pimpri, Pune, 411018, India.; School of Pharmacy and Research, Dnyaan Prasad Global University, Pimpri, Pune, India., Labhade S; Dr. D.Y. Patil Institute of Pharmaceutical Sciences and Research, Pimpri, Pune, 411018, India.; School of Pharmacy and Research, Dnyaan Prasad Global University, Pimpri, Pune, India., Sakle N; Y. B. Chavan College of Pharmacy, Dr. Rafiq Zakaria Campus, Chh. Sambhajinagar, 431001, Maharashtra, India., Bhole R; Dr. D.Y. Patil Institute of Pharmaceutical Sciences and Research, Pimpri, Pune, 411018, India.; Dr. D.Y. Patil Dental College and Hospital, Dr. D.Y. Patil Vidyapeeth, Pimpri, Pune, Maharashtra, India., Kapare H; Dr. D.Y. Patil Institute of Pharmaceutical Sciences and Research, Pimpri, Pune, 411018, India.; School of Pharmacy and Research, Dnyaan Prasad Global University, Pimpri, Pune, India.
Source: Biochemical genetics [Biochem Genet] 2026 Apr 11. Date of Electronic Publication: 2026 Apr 11.
Publication Type: Journal Article; Review
Journal Info: Publisher: Kluwer Academic/Plenum Publishers Country of Publication: United States NLM ID: 0126611 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1573-4927 (Electronic) Linking ISSN: 00062928 NLM ISO Abbreviation: Biochem Genet Subsets: MEDLINE
Database: MEDLINE Ultimate
Description
ISSN:1573-4927
DOI:10.1007/s10528-026-11378-2