Next-Generation Therapies for Genetic Diseases: The Synergy of CRISPR and Gene Therapy.

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Title: Next-Generation Therapies for Genetic Diseases: The Synergy of CRISPR and Gene Therapy.
Authors: Karwa P; Dr. D.Y. Patil Institute of Pharmaceutical Sciences and Research, Pimpri, Pune, 411018, India. pawan.karwa@dypvp.edu.in.; School of Pharmacy and Research, Dnyaan Prasad Global University, Pimpri, Pune, India. pawan.karwa@dypvp.edu.in., Kharul A; Dr. D.Y. Patil Institute of Pharmaceutical Sciences and Research, Pimpri, Pune, 411018, India.; School of Pharmacy and Research, Dnyaan Prasad Global University, Pimpri, Pune, India., Parekar V; Dr. D.Y. Patil Institute of Pharmaceutical Sciences and Research, Pimpri, Pune, 411018, India.; School of Pharmacy and Research, Dnyaan Prasad Global University, Pimpri, Pune, India., Labhade S; Dr. D.Y. Patil Institute of Pharmaceutical Sciences and Research, Pimpri, Pune, 411018, India.; School of Pharmacy and Research, Dnyaan Prasad Global University, Pimpri, Pune, India., Sakle N; Y. B. Chavan College of Pharmacy, Dr. Rafiq Zakaria Campus, Chh. Sambhajinagar, 431001, Maharashtra, India., Bhole R; Dr. D.Y. Patil Institute of Pharmaceutical Sciences and Research, Pimpri, Pune, 411018, India.; Dr. D.Y. Patil Dental College and Hospital, Dr. D.Y. Patil Vidyapeeth, Pimpri, Pune, Maharashtra, India., Kapare H; Dr. D.Y. Patil Institute of Pharmaceutical Sciences and Research, Pimpri, Pune, 411018, India.; School of Pharmacy and Research, Dnyaan Prasad Global University, Pimpri, Pune, India.
Source: Biochemical genetics [Biochem Genet] 2026 Apr 11. Date of Electronic Publication: 2026 Apr 11.
Publication Type: Journal Article; Review
Journal Info: Publisher: Kluwer Academic/Plenum Publishers Country of Publication: United States NLM ID: 0126611 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1573-4927 (Electronic) Linking ISSN: 00062928 NLM ISO Abbreviation: Biochem Genet Subsets: MEDLINE
Database: MEDLINE Ultimate
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  Data: Next-Generation Therapies for Genetic Diseases: The Synergy of CRISPR and Gene Therapy.
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  Data: <searchLink fieldCode="AU" term="%22Karwa+P%22">Karwa P</searchLink>; Dr. D.Y. Patil Institute of Pharmaceutical Sciences and Research, Pimpri, Pune, 411018, India. pawan.karwa@dypvp.edu.in.; School of Pharmacy and Research, Dnyaan Prasad Global University, Pimpri, Pune, India. pawan.karwa@dypvp.edu.in.<br /><searchLink fieldCode="AU" term="%22Kharul+A%22">Kharul A</searchLink>; Dr. D.Y. Patil Institute of Pharmaceutical Sciences and Research, Pimpri, Pune, 411018, India.; School of Pharmacy and Research, Dnyaan Prasad Global University, Pimpri, Pune, India.<br /><searchLink fieldCode="AU" term="%22Parekar+V%22">Parekar V</searchLink>; Dr. D.Y. Patil Institute of Pharmaceutical Sciences and Research, Pimpri, Pune, 411018, India.; School of Pharmacy and Research, Dnyaan Prasad Global University, Pimpri, Pune, India.<br /><searchLink fieldCode="AU" term="%22Labhade+S%22">Labhade S</searchLink>; Dr. D.Y. Patil Institute of Pharmaceutical Sciences and Research, Pimpri, Pune, 411018, India.; School of Pharmacy and Research, Dnyaan Prasad Global University, Pimpri, Pune, India.<br /><searchLink fieldCode="AU" term="%22Sakle+N%22">Sakle N</searchLink>; Y. B. Chavan College of Pharmacy, Dr. Rafiq Zakaria Campus, Chh. Sambhajinagar, 431001, Maharashtra, India.<br /><searchLink fieldCode="AU" term="%22Bhole+R%22">Bhole R</searchLink>; Dr. D.Y. Patil Institute of Pharmaceutical Sciences and Research, Pimpri, Pune, 411018, India.; Dr. D.Y. Patil Dental College and Hospital, Dr. D.Y. Patil Vidyapeeth, Pimpri, Pune, Maharashtra, India.<br /><searchLink fieldCode="AU" term="%22Kapare+H%22">Kapare H</searchLink>; Dr. D.Y. Patil Institute of Pharmaceutical Sciences and Research, Pimpri, Pune, 411018, India.; School of Pharmacy and Research, Dnyaan Prasad Global University, Pimpri, Pune, India.
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  Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Kluwer+Academic%2FPlenum+Publishers%22">Kluwer Academic/Plenum Publishers </searchLink><i>Country of Publication: </i>United States <i>NLM ID: </i>0126611 <i>Publication Model: </i>Print-Electronic <i>Cited Medium: </i>Internet <i>ISSN: </i>1573-4927 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2200062928%22">00062928 </searchLink><i>NLM ISO Abbreviation: </i>Biochem Genet <i>Subsets: </i>MEDLINE
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        Value: 10.1007/s10528-026-11378-2
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        Text: English
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            – D: 11
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              Text: 2026 Apr 11
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