From Gene to Hope: Rett Syndrome and the Rise of Molecular Therapies.

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Title: From Gene to Hope: Rett Syndrome and the Rise of Molecular Therapies.
Authors: Leblay Y; Université Paris Cité, CNRS, Saints-Pères Paris Institute for the Neurosciences, 75006, Paris, France., Felix MS; Aix Marseille Univ, INSERM, MMG, U1251, Faculté de Médecine Timone, 13005, Marseille, France., Roux JC; INMED, INSERM, Aix Marseille University, 13273, Marseille, France. jean-christophe.roux@univ-amu.fr., Panayotis N; Université Paris Cité, CNRS, Saints-Pères Paris Institute for the Neurosciences, 75006, Paris, France. nicolas.panayotis@u-paris.fr.
Source: Molecular diagnosis & therapy [Mol Diagn Ther] 2026 Jul; Vol. 30 (4), pp. 575-585. Date of Electronic Publication: 2026 Apr 13.
Publication Type: Journal Article; Review; Research Support, Non-U.S. Gov't
Journal Info: Publisher: Adis, Springer International Country of Publication: New Zealand NLM ID: 101264260 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1179-2000 (Electronic) Linking ISSN: 11771062 NLM ISO Abbreviation: Mol Diagn Ther Subsets: MEDLINE
Database: MEDLINE Ultimate
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  Data: From Gene to Hope: Rett Syndrome and the Rise of Molecular Therapies.
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  Data: <searchLink fieldCode="AU" term="%22Leblay+Y%22">Leblay Y</searchLink>; Université Paris Cité, CNRS, Saints-Pères Paris Institute for the Neurosciences, 75006, Paris, France.<br /><searchLink fieldCode="AU" term="%22Felix+MS%22">Felix MS</searchLink>; Aix Marseille Univ, INSERM, MMG, U1251, Faculté de Médecine Timone, 13005, Marseille, France.<br /><searchLink fieldCode="AU" term="%22Roux+JC%22">Roux JC</searchLink>; INMED, INSERM, Aix Marseille University, 13273, Marseille, France. jean-christophe.roux@univ-amu.fr.<br /><searchLink fieldCode="AU" term="%22Panayotis+N%22">Panayotis N</searchLink>; Université Paris Cité, CNRS, Saints-Pères Paris Institute for the Neurosciences, 75006, Paris, France. nicolas.panayotis@u-paris.fr.
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  Data: <searchLink fieldCode="JN" term="%22101264260%22">Molecular diagnosis & therapy</searchLink> [Mol Diagn Ther] 2026 Jul; Vol. 30 (4), pp. 575-585. <i>Date of Electronic Publication: </i>2026 Apr 13.
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  Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Adis%2C+Springer+International%22">Adis, Springer International </searchLink><i>Country of Publication: </i>New Zealand <i>NLM ID: </i>101264260 <i>Publication Model: </i>Print-Electronic <i>Cited Medium: </i>Internet <i>ISSN: </i>1179-2000 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2211771062%22">11771062 </searchLink><i>NLM ISO Abbreviation: </i>Mol Diagn Ther <i>Subsets: </i>MEDLINE
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        Value: 10.1007/s40291-026-00847-4
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      – Code: eng
        Text: English
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              Text: 2026 Jul
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              Y: 2026
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