Clinical outcomes of lentiviral vector gene therapy for sickle cell disease.

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Title: Clinical outcomes of lentiviral vector gene therapy for sickle cell disease.
Authors: Prueksapraopong C; Department of Pediatrics, Hematology/Oncology, David Geffen School of Medicine, University of California, Los Angeles, CA., Fernandes A; Department of Microbiology, Immunology, and Molecular Genetics, David Geffen School of Medicine, University of California, Los Angeles, CA., Campo Fernandez B; Department of Microbiology, Immunology, and Molecular Genetics, David Geffen School of Medicine, University of California, Los Angeles, CA., Roy S; Department of Microbiology, Immunology, and Molecular Genetics, David Geffen School of Medicine, University of California, Los Angeles, CA., Hollis RP; Department of Microbiology, Immunology, and Molecular Genetics, David Geffen School of Medicine, University of California, Los Angeles, CA., Habtemariam B; Department of Medicine, Hematology/Oncology, David Geffen School of Medicine, University of California, Los Angeles, CA., Pellin D; Gene Therapy Program, Dana-Farber/Boston Children's Cancer and Blood Disorders Center, Harvard Medical School, Boston, MA., Ceoldo G; Gene Therapy Program, Dana-Farber/Boston Children's Cancer and Blood Disorders Center, Harvard Medical School, Boston, MA., Lin TY; Department of Medical and Molecular Genetics, Indiana University School of Medicine, Indianapolis, IN., Dang TT; Department of Medical and Molecular Genetics, Indiana University School of Medicine, Indianapolis, IN., Cornetta K; Department of Medical and Molecular Genetics, Indiana University School of Medicine, Indianapolis, IN., Romero Z; Department of Microbiology, Immunology, and Molecular Genetics, David Geffen School of Medicine, University of California, Los Angeles, CA., Blazar BR; Division of Pediatric Blood and Marrow Transplant & Cellular Therapy, Department of Pediatrics, University of Minnesota, Minneapolis, MN., Shah AJ; Division of Pediatric Hematology, Oncology, Stem Cell Transplantation & Regenerative Medicine, Stanford School of Medicine, Palo Alto, CA., Moore TB; Department of Pediatrics, Hematology/Oncology, David Geffen School of Medicine, University of California, Los Angeles, CA., Sehl M; Department of Medicine, Hematology/Oncology, David Geffen School of Medicine, University of California, Los Angeles, CA., Schiller GJ; Department of Medicine, Hematology/Oncology, David Geffen School of Medicine, University of California, Los Angeles, CA., Kohn DB; Department of Pediatrics, Hematology/Oncology, David Geffen School of Medicine, University of California, Los Angeles, CA.; Department of Microbiology, Immunology, and Molecular Genetics, David Geffen School of Medicine, University of California, Los Angeles, CA.; The Eli and Edythe Broad Center of Regeneration Medicine and Stem Cell Research, University of California, Los Angeles, CA.
Source: Blood advances [Blood Adv] 2026 Jul 28; Vol. 10 (14), pp. 4991-5002.
Publication Type: Journal Article; Clinical Trial, Phase I; Clinical Trial, Phase II
Journal Info: Publisher: American Society of Hematology Country of Publication: United States NLM ID: 101698425 Publication Model: Print Cited Medium: Internet ISSN: 2473-9537 (Electronic) Linking ISSN: 24739529 NLM ISO Abbreviation: Blood Adv Subsets: MEDLINE
Database: MEDLINE Ultimate
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  Data: Clinical outcomes of lentiviral vector gene therapy for sickle cell disease.
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  Data: <searchLink fieldCode="AU" term="%22Prueksapraopong+C%22">Prueksapraopong C</searchLink>; Department of Pediatrics, Hematology/Oncology, David Geffen School of Medicine, University of California, Los Angeles, CA.<br /><searchLink fieldCode="AU" term="%22Fernandes+A%22">Fernandes A</searchLink>; Department of Microbiology, Immunology, and Molecular Genetics, David Geffen School of Medicine, University of California, Los Angeles, CA.<br /><searchLink fieldCode="AU" term="%22Campo+Fernandez+B%22">Campo Fernandez B</searchLink>; Department of Microbiology, Immunology, and Molecular Genetics, David Geffen School of Medicine, University of California, Los Angeles, CA.<br /><searchLink fieldCode="AU" term="%22Roy+S%22">Roy S</searchLink>; Department of Microbiology, Immunology, and Molecular Genetics, David Geffen School of Medicine, University of California, Los Angeles, CA.<br /><searchLink fieldCode="AU" term="%22Hollis+RP%22">Hollis RP</searchLink>; Department of Microbiology, Immunology, and Molecular Genetics, David Geffen School of Medicine, University of California, Los Angeles, CA.<br /><searchLink fieldCode="AU" term="%22Habtemariam+B%22">Habtemariam B</searchLink>; Department of Medicine, Hematology/Oncology, David Geffen School of Medicine, University of California, Los Angeles, CA.<br /><searchLink fieldCode="AU" term="%22Pellin+D%22">Pellin D</searchLink>; Gene Therapy Program, Dana-Farber/Boston Children's Cancer and Blood Disorders Center, Harvard Medical School, Boston, MA.<br /><searchLink fieldCode="AU" term="%22Ceoldo+G%22">Ceoldo G</searchLink>; Gene Therapy Program, Dana-Farber/Boston Children's Cancer and Blood Disorders Center, Harvard Medical School, Boston, MA.<br /><searchLink fieldCode="AU" term="%22Lin+TY%22">Lin TY</searchLink>; Department of Medical and Molecular Genetics, Indiana University School of Medicine, Indianapolis, IN.<br /><searchLink fieldCode="AU" term="%22Dang+TT%22">Dang TT</searchLink>; Department of Medical and Molecular Genetics, Indiana University School of Medicine, Indianapolis, IN.<br /><searchLink fieldCode="AU" term="%22Cornetta+K%22">Cornetta K</searchLink>; Department of Medical and Molecular Genetics, Indiana University School of Medicine, Indianapolis, IN.<br /><searchLink fieldCode="AU" term="%22Romero+Z%22">Romero Z</searchLink>; Department of Microbiology, Immunology, and Molecular Genetics, David Geffen School of Medicine, University of California, Los Angeles, CA.<br /><searchLink fieldCode="AU" term="%22Blazar+BR%22">Blazar BR</searchLink>; Division of Pediatric Blood and Marrow Transplant & Cellular Therapy, Department of Pediatrics, University of Minnesota, Minneapolis, MN.<br /><searchLink fieldCode="AU" term="%22Shah+AJ%22">Shah AJ</searchLink>; Division of Pediatric Hematology, Oncology, Stem Cell Transplantation & Regenerative Medicine, Stanford School of Medicine, Palo Alto, CA.<br /><searchLink fieldCode="AU" term="%22Moore+TB%22">Moore TB</searchLink>; Department of Pediatrics, Hematology/Oncology, David Geffen School of Medicine, University of California, Los Angeles, CA.<br /><searchLink fieldCode="AU" term="%22Sehl+M%22">Sehl M</searchLink>; Department of Medicine, Hematology/Oncology, David Geffen School of Medicine, University of California, Los Angeles, CA.<br /><searchLink fieldCode="AU" term="%22Schiller+GJ%22">Schiller GJ</searchLink>; Department of Medicine, Hematology/Oncology, David Geffen School of Medicine, University of California, Los Angeles, CA.<br /><searchLink fieldCode="AU" term="%22Kohn+DB%22">Kohn DB</searchLink>; Department of Pediatrics, Hematology/Oncology, David Geffen School of Medicine, University of California, Los Angeles, CA.; Department of Microbiology, Immunology, and Molecular Genetics, David Geffen School of Medicine, University of California, Los Angeles, CA.; The Eli and Edythe Broad Center of Regeneration Medicine and Stem Cell Research, University of California, Los Angeles, CA.
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  Data: <searchLink fieldCode="JN" term="%22101698425%22">Blood advances</searchLink> [Blood Adv] 2026 Jul 28; Vol. 10 (14), pp. 4991-5002.
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  Data: Journal Article; Clinical Trial, Phase I; Clinical Trial, Phase II
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  Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22American+Society+of+Hematology%22">American Society of Hematology </searchLink><i>Country of Publication: </i>United States <i>NLM ID: </i>101698425 <i>Publication Model: </i>Print <i>Cited Medium: </i>Internet <i>ISSN: </i>2473-9537 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2224739529%22">24739529 </searchLink><i>NLM ISO Abbreviation: </i>Blood Adv <i>Subsets: </i>MEDLINE
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        Value: 10.1182/bloodadvances.2026019869
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