Design and Validation of Mirtron-Mediated RNA Interference for Gene Therapy.
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| Title: | Design and Validation of Mirtron-Mediated RNA Interference for Gene Therapy. |
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| Authors: | Zheng Q; Nuffield Department of Clinical Neurosciences & NIHR Oxford Biomedical Research Centre, University of Oxford, UK and Oxford Eye Hospital, Oxford University Hospitals NHS Foundation Trust, Oxford, UK., Orlans HO; Nuffield Department of Clinical Neurosciences & NIHR Oxford Biomedical Research Centre, University of Oxford, UK and Oxford Eye Hospital, Oxford University Hospitals NHS Foundation Trust, Oxford, UK., Staurenghi F; Nuffield Department of Clinical Neurosciences & NIHR Oxford Biomedical Research Centre, University of Oxford, UK and Oxford Eye Hospital, Oxford University Hospitals NHS Foundation Trust, Oxford, UK., McClements ME; Nuffield Department of Clinical Neurosciences & NIHR Oxford Biomedical Research Centre, University of Oxford, UK and Oxford Eye Hospital, Oxford University Hospitals NHS Foundation Trust, Oxford, UK., MacLaren RE; Nuffield Department of Clinical Neurosciences & NIHR Oxford Biomedical Research Centre, University of Oxford, UK and Oxford Eye Hospital, Oxford University Hospitals NHS Foundation Trust, Oxford, UK. maclaren@eye.ox.ac.uk. |
| Source: | Methods in molecular biology (Clifton, N.J.) [Methods Mol Biol] 2026; Vol. 3023, pp. 195-206. |
| Publication Type: | Journal Article |
| Journal Info: | Publisher: Humana Press Country of Publication: United States NLM ID: 9214969 Publication Model: Print Cited Medium: Internet ISSN: 1940-6029 (Electronic) Linking ISSN: 10643745 NLM ISO Abbreviation: Methods Mol Biol Subsets: MEDLINE |
| Database: | MEDLINE Ultimate |
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