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Imlifidase enables AAV gene therapy in a seropositive Crigler-Najjar patient: On the verge of a paradigm shift.

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Title: Imlifidase enables AAV gene therapy in a seropositive Crigler-Najjar patient: On the verge of a paradigm shift.
Authors: Do Cao J; APHP, Université Paris Saclay, Hôpital Antoine Béclère, CRMR Maladies Héréditaires du Métabolisme Hépatique, Clamart, France; Filière nationale de santé maladies rares G2M-Maladies Héréditaires du Métabolisme, Paris, France. Electronic address: jeremy.do-cao@aphp.fr., Gao-Desliens J; Genethon, 1 bis rue de l'Internationale, 91000 Evry-Courcouronnes, France., Valent A; Genethon, 1 bis rue de l'Internationale, 91000 Evry-Courcouronnes, France., Knuchel-Legendre N; Genethon, 1 bis rue de l'Internationale, 91000 Evry-Courcouronnes, France., Colpin C; Genethon, 1 bis rue de l'Internationale, 91000 Evry-Courcouronnes, France., Guyon H; Genethon, 1 bis rue de l'Internationale, 91000 Evry-Courcouronnes, France., Winstedt L; Hansa Biopharma, 223 63 Lund, Sweden., Leborgne C; Genethon, 1 bis rue de l'Internationale, 91000 Evry-Courcouronnes, France., Perret G; Genethon, 1 bis rue de l'Internationale, 91000 Evry-Courcouronnes, France., Ronzitti G; Genethon, 1 bis rue de l'Internationale, 91000 Evry-Courcouronnes, France., Labrune P; APHP, Université Paris Saclay, Hôpital Antoine Béclère, CRMR Maladies Héréditaires du Métabolisme Hépatique, Clamart, France; Filière nationale de santé maladies rares G2M-Maladies Héréditaires du Métabolisme, Paris, France; Faculté de médecine, Université Paris Saclay, 63 Rue Gabriel Péri, 94270 Le Kremlin-Bicêtre, France.
Source: Molecular therapy : the journal of the American Society of Gene Therapy [Mol Ther] 2026 May 06; Vol. 34 (5), pp. 2571-2572. Date of Electronic Publication: 2026 Apr 27.
Publication Type: Journal Article
Journal Info: Publisher: Cell Press Country of Publication: United States NLM ID: 100890581 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1525-0024 (Electronic) Linking ISSN: 15250016 NLM ISO Abbreviation: Mol Ther Subsets: MEDLINE; In Process
Database: MEDLINE Ultimate
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  Data: Imlifidase enables AAV gene therapy in a seropositive Crigler-Najjar patient: On the verge of a paradigm shift.
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  Data: <searchLink fieldCode="AU" term="%22Do+Cao+J%22">Do Cao J</searchLink>; APHP, Université Paris Saclay, Hôpital Antoine Béclère, CRMR Maladies Héréditaires du Métabolisme Hépatique, Clamart, France; Filière nationale de santé maladies rares G2M-Maladies Héréditaires du Métabolisme, Paris, France. Electronic address: jeremy.do-cao@aphp.fr.<br /><searchLink fieldCode="AU" term="%22Gao-Desliens+J%22">Gao-Desliens J</searchLink>; Genethon, 1 bis rue de l'Internationale, 91000 Evry-Courcouronnes, France.<br /><searchLink fieldCode="AU" term="%22Valent+A%22">Valent A</searchLink>; Genethon, 1 bis rue de l'Internationale, 91000 Evry-Courcouronnes, France.<br /><searchLink fieldCode="AU" term="%22Knuchel-Legendre+N%22">Knuchel-Legendre N</searchLink>; Genethon, 1 bis rue de l'Internationale, 91000 Evry-Courcouronnes, France.<br /><searchLink fieldCode="AU" term="%22Colpin+C%22">Colpin C</searchLink>; Genethon, 1 bis rue de l'Internationale, 91000 Evry-Courcouronnes, France.<br /><searchLink fieldCode="AU" term="%22Guyon+H%22">Guyon H</searchLink>; Genethon, 1 bis rue de l'Internationale, 91000 Evry-Courcouronnes, France.<br /><searchLink fieldCode="AU" term="%22Winstedt+L%22">Winstedt L</searchLink>; Hansa Biopharma, 223 63 Lund, Sweden.<br /><searchLink fieldCode="AU" term="%22Leborgne+C%22">Leborgne C</searchLink>; Genethon, 1 bis rue de l'Internationale, 91000 Evry-Courcouronnes, France.<br /><searchLink fieldCode="AU" term="%22Perret+G%22">Perret G</searchLink>; Genethon, 1 bis rue de l'Internationale, 91000 Evry-Courcouronnes, France.<br /><searchLink fieldCode="AU" term="%22Ronzitti+G%22">Ronzitti G</searchLink>; Genethon, 1 bis rue de l'Internationale, 91000 Evry-Courcouronnes, France.<br /><searchLink fieldCode="AU" term="%22Labrune+P%22">Labrune P</searchLink>; APHP, Université Paris Saclay, Hôpital Antoine Béclère, CRMR Maladies Héréditaires du Métabolisme Hépatique, Clamart, France; Filière nationale de santé maladies rares G2M-Maladies Héréditaires du Métabolisme, Paris, France; Faculté de médecine, Université Paris Saclay, 63 Rue Gabriel Péri, 94270 Le Kremlin-Bicêtre, France.
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  Data: <searchLink fieldCode="JN" term="%22100890581%22">Molecular therapy : the journal of the American Society of Gene Therapy</searchLink> [Mol Ther] 2026 May 06; Vol. 34 (5), pp. 2571-2572. <i>Date of Electronic Publication: </i>2026 Apr 27.
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  Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Cell+Press%22">Cell Press </searchLink><i>Country of Publication: </i>United States <i>NLM ID: </i>100890581 <i>Publication Model: </i>Print-Electronic <i>Cited Medium: </i>Internet <i>ISSN: </i>1525-0024 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2215250016%22">15250016 </searchLink><i>NLM ISO Abbreviation: </i>Mol Ther <i>Subsets: </i>MEDLINE; In Process
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              Text: 2026 May 06
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