Population Pharmacokinetic/Pharmacodynamic Modeling of Therapeutic Enzymes in Lysosomal Storage Diseases.

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Bibliographic Details
Title: Population Pharmacokinetic/Pharmacodynamic Modeling of Therapeutic Enzymes in Lysosomal Storage Diseases.
Authors: Barzel I; Department of Hospital Pharmacy, Erasmus MC, Erasmus University Medical Center, Dr. Molewaterplein 40, 3015 GD, Rotterdam, The Netherlands. i.barzel@erasmusmc.nl.; Rotterdam Clinical Pharmacometrics Group, Erasmus MC, Erasmus University Medical Center, Rotterdam, The Netherlands. i.barzel@erasmusmc.nl., van der Ploeg AT; Department of Pediatrics, Erasmus MC, Erasmus University Medical Center, Rotterdam, The Netherlands.; Center for Lysosomal and Metabolic Diseases, Erasmus MC, Erasmus University Medical Center, Rotterdam, The Netherlands., Pijnappel WWMP; Department of Pediatrics, Erasmus MC, Erasmus University Medical Center, Rotterdam, The Netherlands.; Department of Clinical Genetics, Erasmus MC, Erasmus University Medical Center, Rotterdam, The Netherlands.; Center for Lysosomal and Metabolic Diseases, Erasmus MC, Erasmus University Medical Center, Rotterdam, The Netherlands., van der Kuy PHM; Department of Hospital Pharmacy, Erasmus MC, Erasmus University Medical Center, Dr. Molewaterplein 40, 3015 GD, Rotterdam, The Netherlands., van den Hout JMP; Department of Pediatrics, Erasmus MC, Erasmus University Medical Center, Rotterdam, The Netherlands.; Center for Lysosomal and Metabolic Diseases, Erasmus MC, Erasmus University Medical Center, Rotterdam, The Netherlands., Preijers T; Department of Hospital Pharmacy, Erasmus MC, Erasmus University Medical Center, Dr. Molewaterplein 40, 3015 GD, Rotterdam, The Netherlands.; Rotterdam Clinical Pharmacometrics Group, Erasmus MC, Erasmus University Medical Center, Rotterdam, The Netherlands.
Source: Clinical pharmacokinetics [Clin Pharmacokinet] 2026 May; Vol. 65 (5), pp. 647-664. Date of Electronic Publication: 2026 May 08.
Publication Type: Journal Article; Review; Systematic Review
Journal Info: Publisher: Country of Publication: Switzerland NLM ID: 7606849 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1179-1926 (Electronic) Linking ISSN: 03125963 NLM ISO Abbreviation: Clin Pharmacokinet Subsets: MEDLINE
Database: MEDLINE Ultimate
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