Optimising Formulations for Paediatric Patients with Inherited Metabolic Disorders: The Case Study of Levocarnitine.

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Title: Optimising Formulations for Paediatric Patients with Inherited Metabolic Disorders: The Case Study of Levocarnitine.
Authors: Tomlin S; Director Children's Medicines Research and Innovation Centre, Great Ormond Street Hospital for Children, London, WC1N 1EP, UK., Mühlhausen C; Department of Paediatrics and Adolescent Medicine, University Medical Center, Georg-August University, Göttingen, Germany., Krendyukov A; Medical Office, Aspire Pharma Ltd., 4 Rotherbrook Court, Bedford Road, Petersfield, Hampshire, UK. ankov.de@outlook.com., Das AM; Department of Paediatrics, Clinic for Paediatric Kidney, Liver- and Metabolic Diseases and Neuropaediatrics, Hannover Medical School, Carl Neuberg Str. 1, 30625, Hannover, Germany.
Source: Pharmaceutical medicine [Pharmaceut Med] 2026 Jul; Vol. 40 (4), pp. 275-285. Date of Electronic Publication: 2026 Jun 04.
Publication Type: Journal Article; Review
Journal Info: Publisher: Adis, Springer International Country of Publication: New Zealand NLM ID: 101471195 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1179-1993 (Electronic) Linking ISSN: 11782595 NLM ISO Abbreviation: Pharmaceut Med Subsets: MEDLINE
Database: MEDLINE Ultimate
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  Data: <searchLink fieldCode="AU" term="%22Tomlin+S%22">Tomlin S</searchLink>; Director Children's Medicines Research and Innovation Centre, Great Ormond Street Hospital for Children, London, WC1N 1EP, UK.<br /><searchLink fieldCode="AU" term="%22Mühlhausen+C%22">Mühlhausen C</searchLink>; Department of Paediatrics and Adolescent Medicine, University Medical Center, Georg-August University, Göttingen, Germany.<br /><searchLink fieldCode="AU" term="%22Krendyukov+A%22">Krendyukov A</searchLink>; Medical Office, Aspire Pharma Ltd., 4 Rotherbrook Court, Bedford Road, Petersfield, Hampshire, UK. ankov.de@outlook.com.<br /><searchLink fieldCode="AU" term="%22Das+AM%22">Das AM</searchLink>; Department of Paediatrics, Clinic for Paediatric Kidney, Liver- and Metabolic Diseases and Neuropaediatrics, Hannover Medical School, Carl Neuberg Str. 1, 30625, Hannover, Germany.
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  Data: <searchLink fieldCode="JN" term="%22101471195%22">Pharmaceutical medicine</searchLink> [Pharmaceut Med] 2026 Jul; Vol. 40 (4), pp. 275-285. <i>Date of Electronic Publication: </i>2026 Jun 04.
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  Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Adis%2C+Springer+International%22">Adis, Springer International </searchLink><i>Country of Publication: </i>New Zealand <i>NLM ID: </i>101471195 <i>Publication Model: </i>Print-Electronic <i>Cited Medium: </i>Internet <i>ISSN: </i>1179-1993 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2211782595%22">11782595 </searchLink><i>NLM ISO Abbreviation: </i>Pharmaceut Med <i>Subsets: </i>MEDLINE
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        Value: 10.1007/s40290-026-00611-3
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        Text: English
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      – TitleFull: Optimising Formulations for Paediatric Patients with Inherited Metabolic Disorders: The Case Study of Levocarnitine.
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              Text: 2026 Jul
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