Ora visual navigation course™ mobility test results in two individuals with CEP290 LCA after intravitreal injection of antisense oligonucleotide.

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Title: Ora visual navigation course™ mobility test results in two individuals with CEP290 LCA after intravitreal injection of antisense oligonucleotide.
Authors: Marques C; Department of Ophthalmology and Visual Sciences, Universidade Federal de São Paulo, Escola Paulista de Medicina, São Paulo, Brazil.; Instituto de Genética Ocular, São Paulo, Brazil., Rodrigues GD; Department of Ophthalmology and Visual Sciences, Universidade Federal de São Paulo, Escola Paulista de Medicina, São Paulo, Brazil.; Instituto de Genética Ocular, São Paulo, Brazil., da Silva Martins EA; Department of Ophthalmology and Visual Sciences, Universidade Federal de São Paulo, Escola Paulista de Medicina, São Paulo, Brazil., Soares Nunes PH; Department of Ophthalmology and Visual Sciences, Universidade Federal de São Paulo, Escola Paulista de Medicina, São Paulo, Brazil.; Instituto de Genética Ocular, São Paulo, Brazil., Silva LMPD; Department of Ophthalmology and Visual Sciences, Universidade Federal de São Paulo, Escola Paulista de Medicina, São Paulo, Brazil., Muccioli C; Department of Ophthalmology and Visual Sciences, Universidade Federal de São Paulo, Escola Paulista de Medicina, São Paulo, Brazil., Berezovsky A; Department of Ophthalmology and Visual Sciences, Universidade Federal de São Paulo, Escola Paulista de Medicina, São Paulo, Brazil., Ferraz NN; Department of Ophthalmology and Visual Sciences, Universidade Federal de São Paulo, Escola Paulista de Medicina, São Paulo, Brazil., Sacai PY; Department of Ophthalmology and Visual Sciences, Universidade Federal de São Paulo, Escola Paulista de Medicina, São Paulo, Brazil., Salles MV; Department of Ophthalmology and Visual Sciences, Universidade Federal de São Paulo, Escola Paulista de Medicina, São Paulo, Brazil.; Instituto de Genética Ocular, São Paulo, Brazil., Amaral RAS; Department of Ophthalmology and Visual Sciences, Universidade Federal de São Paulo, Escola Paulista de Medicina, São Paulo, Brazil.; Instituto de Genética Ocular, São Paulo, Brazil., da Palma MM; Department of Ophthalmology and Visual Sciences, Universidade Federal de São Paulo, Escola Paulista de Medicina, São Paulo, Brazil.; Instituto de Genética Ocular, São Paulo, Brazil., Yasaki ÉS; Department of Ophthalmology and Visual Sciences, Universidade Federal de São Paulo, Escola Paulista de Medicina, São Paulo, Brazil., Vasconcelos Junior HM; Department of Ophthalmology and Visual Sciences, Universidade Federal de São Paulo, Escola Paulista de Medicina, São Paulo, Brazil.; Instituto de Genética Ocular, São Paulo, Brazil., Toro F; Ora LLC, Andover, Massachusetts, USA., Sundstrom C; Ora LLC, Andover, Massachusetts, USA., Caka M; Ora LLC, Andover, Massachusetts, USA., Schwartz MR; Sepul Bio, Laboratoires THEA, Clermont-Ferrand, France., Butuner Z; Sepul Bio, Laboratoires THEA, Clermont-Ferrand, France., Sallum JMF; Department of Ophthalmology and Visual Sciences, Universidade Federal de São Paulo, Escola Paulista de Medicina, São Paulo, Brazil.; Instituto de Genética Ocular, São Paulo, Brazil.
Source: Ophthalmic genetics [Ophthalmic Genet] 2026 Jun 24, pp. 1-7. Date of Electronic Publication: 2026 Jun 24.
Publication Type: Journal Article
Journal Info: Publisher: Informa Healthcare Country of Publication: England NLM ID: 9436057 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1744-5094 (Electronic) Linking ISSN: 13816810 NLM ISO Abbreviation: Ophthalmic Genet Subsets: MEDLINE
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  Data: Ora visual navigation course™ mobility test results in two individuals with CEP290 LCA after intravitreal injection of antisense oligonucleotide.
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  Data: <searchLink fieldCode="AU" term="%22Marques+C%22">Marques C</searchLink>; Department of Ophthalmology and Visual Sciences, Universidade Federal de São Paulo, Escola Paulista de Medicina, São Paulo, Brazil.; Instituto de Genética Ocular, São Paulo, Brazil.<br /><searchLink fieldCode="AU" term="%22Rodrigues+GD%22">Rodrigues GD</searchLink>; Department of Ophthalmology and Visual Sciences, Universidade Federal de São Paulo, Escola Paulista de Medicina, São Paulo, Brazil.; Instituto de Genética Ocular, São Paulo, Brazil.<br /><searchLink fieldCode="AU" term="%22da+Silva+Martins+EA%22">da Silva Martins EA</searchLink>; Department of Ophthalmology and Visual Sciences, Universidade Federal de São Paulo, Escola Paulista de Medicina, São Paulo, Brazil.<br /><searchLink fieldCode="AU" term="%22Soares+Nunes+PH%22">Soares Nunes PH</searchLink>; Department of Ophthalmology and Visual Sciences, Universidade Federal de São Paulo, Escola Paulista de Medicina, São Paulo, Brazil.; Instituto de Genética Ocular, São Paulo, Brazil.<br /><searchLink fieldCode="AU" term="%22Silva+LMPD%22">Silva LMPD</searchLink>; Department of Ophthalmology and Visual Sciences, Universidade Federal de São Paulo, Escola Paulista de Medicina, São Paulo, Brazil.<br /><searchLink fieldCode="AU" term="%22Muccioli+C%22">Muccioli C</searchLink>; Department of Ophthalmology and Visual Sciences, Universidade Federal de São Paulo, Escola Paulista de Medicina, São Paulo, Brazil.<br /><searchLink fieldCode="AU" term="%22Berezovsky+A%22">Berezovsky A</searchLink>; Department of Ophthalmology and Visual Sciences, Universidade Federal de São Paulo, Escola Paulista de Medicina, São Paulo, Brazil.<br /><searchLink fieldCode="AU" term="%22Ferraz+NN%22">Ferraz NN</searchLink>; Department of Ophthalmology and Visual Sciences, Universidade Federal de São Paulo, Escola Paulista de Medicina, São Paulo, Brazil.<br /><searchLink fieldCode="AU" term="%22Sacai+PY%22">Sacai PY</searchLink>; Department of Ophthalmology and Visual Sciences, Universidade Federal de São Paulo, Escola Paulista de Medicina, São Paulo, Brazil.<br /><searchLink fieldCode="AU" term="%22Salles+MV%22">Salles MV</searchLink>; Department of Ophthalmology and Visual Sciences, Universidade Federal de São Paulo, Escola Paulista de Medicina, São Paulo, Brazil.; Instituto de Genética Ocular, São Paulo, Brazil.<br /><searchLink fieldCode="AU" term="%22Amaral+RAS%22">Amaral RAS</searchLink>; Department of Ophthalmology and Visual Sciences, Universidade Federal de São Paulo, Escola Paulista de Medicina, São Paulo, Brazil.; Instituto de Genética Ocular, São Paulo, Brazil.<br /><searchLink fieldCode="AU" term="%22da+Palma+MM%22">da Palma MM</searchLink>; Department of Ophthalmology and Visual Sciences, Universidade Federal de São Paulo, Escola Paulista de Medicina, São Paulo, Brazil.; Instituto de Genética Ocular, São Paulo, Brazil.<br /><searchLink fieldCode="AU" term="%22Yasaki+ÉS%22">Yasaki ÉS</searchLink>; Department of Ophthalmology and Visual Sciences, Universidade Federal de São Paulo, Escola Paulista de Medicina, São Paulo, Brazil.<br /><searchLink fieldCode="AU" term="%22Vasconcelos+Junior+HM%22">Vasconcelos Junior HM</searchLink>; Department of Ophthalmology and Visual Sciences, Universidade Federal de São Paulo, Escola Paulista de Medicina, São Paulo, Brazil.; Instituto de Genética Ocular, São Paulo, Brazil.<br /><searchLink fieldCode="AU" term="%22Toro+F%22">Toro F</searchLink>; Ora LLC, Andover, Massachusetts, USA.<br /><searchLink fieldCode="AU" term="%22Sundstrom+C%22">Sundstrom C</searchLink>; Ora LLC, Andover, Massachusetts, USA.<br /><searchLink fieldCode="AU" term="%22Caka+M%22">Caka M</searchLink>; Ora LLC, Andover, Massachusetts, USA.<br /><searchLink fieldCode="AU" term="%22Schwartz+MR%22">Schwartz MR</searchLink>; Sepul Bio, Laboratoires THEA, Clermont-Ferrand, France.<br /><searchLink fieldCode="AU" term="%22Butuner+Z%22">Butuner Z</searchLink>; Sepul Bio, Laboratoires THEA, Clermont-Ferrand, France.<br /><searchLink fieldCode="AU" term="%22Sallum+JMF%22">Sallum JMF</searchLink>; Department of Ophthalmology and Visual Sciences, Universidade Federal de São Paulo, Escola Paulista de Medicina, São Paulo, Brazil.; Instituto de Genética Ocular, São Paulo, Brazil.
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