Immunogenic implications of translational readthrough modulate the association of F8 nonsense mutations with inhibitors in Hemophilia A.

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Title: Immunogenic implications of translational readthrough modulate the association of F8 nonsense mutations with inhibitors in Hemophilia A.
Authors: Testa MF; Department of Life Sciences and Biotechnology and LTTA Center, University of Ferrara, Via Fossato di Mortara 74, Ferrara, 44121, Italy., Pinotti M; Department of Life Sciences and Biotechnology and LTTA Center, University of Ferrara, Via Fossato di Mortara 74, Ferrara, 44121, Italy., Branchini A; Department of Life Sciences and Biotechnology and LTTA Center, University of Ferrara, Via Fossato di Mortara 74, Ferrara, 44121, Italy., Mancuso ME; IRCCS, Humanitas Research Hospital, Center for Thrombosis and Hemorrhagic Diseases, Milan, Italy., Bernardi F; Department of Life Sciences and Biotechnology and LTTA Center, University of Ferrara, Via Fossato di Mortara 74, Ferrara, 44121, Italy. ber@unife.it., Balestra D; Department of Life Sciences and Biotechnology and LTTA Center, University of Ferrara, Via Fossato di Mortara 74, Ferrara, 44121, Italy. blsdra@unife.it.
Source: Molecular medicine (Cambridge, Mass.) [Mol Med] 2026 Jun 27. Date of Electronic Publication: 2026 Jun 27.
Publication Type: Journal Article
Journal Info: Publisher: BioMed Central Country of Publication: England NLM ID: 9501023 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1528-3658 (Electronic) Linking ISSN: 10761551 NLM ISO Abbreviation: Mol Med Subsets: MEDLINE
Database: MEDLINE Ultimate
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  Data: Immunogenic implications of translational readthrough modulate the association of F8 nonsense mutations with inhibitors in Hemophilia A.
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  Data: <searchLink fieldCode="AU" term="%22Testa+MF%22">Testa MF</searchLink>; Department of Life Sciences and Biotechnology and LTTA Center, University of Ferrara, Via Fossato di Mortara 74, Ferrara, 44121, Italy.<br /><searchLink fieldCode="AU" term="%22Pinotti+M%22">Pinotti M</searchLink>; Department of Life Sciences and Biotechnology and LTTA Center, University of Ferrara, Via Fossato di Mortara 74, Ferrara, 44121, Italy.<br /><searchLink fieldCode="AU" term="%22Branchini+A%22">Branchini A</searchLink>; Department of Life Sciences and Biotechnology and LTTA Center, University of Ferrara, Via Fossato di Mortara 74, Ferrara, 44121, Italy.<br /><searchLink fieldCode="AU" term="%22Mancuso+ME%22">Mancuso ME</searchLink>; IRCCS, Humanitas Research Hospital, Center for Thrombosis and Hemorrhagic Diseases, Milan, Italy.<br /><searchLink fieldCode="AU" term="%22Bernardi+F%22">Bernardi F</searchLink>; Department of Life Sciences and Biotechnology and LTTA Center, University of Ferrara, Via Fossato di Mortara 74, Ferrara, 44121, Italy. ber@unife.it.<br /><searchLink fieldCode="AU" term="%22Balestra+D%22">Balestra D</searchLink>; Department of Life Sciences and Biotechnology and LTTA Center, University of Ferrara, Via Fossato di Mortara 74, Ferrara, 44121, Italy. blsdra@unife.it.
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  Data: <searchLink fieldCode="JN" term="%229501023%22">Molecular medicine (Cambridge, Mass.)</searchLink> [Mol Med] 2026 Jun 27. <i>Date of Electronic Publication: </i>2026 Jun 27.
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        Value: 10.1186/s10020-026-01536-y
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        Text: English
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      – TitleFull: Immunogenic implications of translational readthrough modulate the association of F8 nonsense mutations with inhibitors in Hemophilia A.
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            NameFull: Testa MF
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            NameFull: Pinotti M
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            – D: 27
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              Text: 2026 Jun 27
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