Clinical Outcomes of Efanesoctocog Alfa Prophylaxis in Children With Severe Haemophilia A: Interim Data From XTEND-ed.

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Bibliographic Details
Title: Clinical Outcomes of Efanesoctocog Alfa Prophylaxis in Children With Severe Haemophilia A: Interim Data From XTEND-ed.
Authors: Malec L; Versiti Blood Research Institute, Milwaukee, Wisconsin, USA.; Division of Hematology & Oncology, Departments of Medicine and Pediatrics, Medical College of Wisconsin, Milwaukee, Wisconsin, USA., Nolan B; Haematology Department, Children's Health Ireland, Dublin, Ireland., Chan AKC; McMaster Children's Hospital, McMaster University, Hamilton, Ontario, Canada., Albisetti M; University Children's Hospital Zurich, Zurich, Switzerland., Chou SC; Department of Internal Medicine, Division of Hematology, National Taiwan University Hospital, College of Medicine, National Taiwan University, Taipei City, Taiwan., Zulfikar B; Division of Pediatric Hematology-Oncology, Istanbul University Oncology Institute, Istanbul, Türkiye., Simpson M; Rush Hemophilia and Thrombophilia Center, Rush University Medical Center, Chicago, Illinois, USA., Feng L; Sanofi, Shanghai, China., Palmborg H; Sobi, Stockholm, Sweden., Neill G; Sanofi, Cambridge, UK., Abad-Franch L; Sobi, Basel, Switzerland., Gunawardena S; Sanofi, Morristown, New Jersey, USA., Fijnvandraat K; Emma Kinderziekenhuis/AMC, University of Amsterdam, Amsterdam, Netherlands.
Source: Haemophilia : the official journal of the World Federation of Hemophilia [Haemophilia] 2026 Jul 04. Date of Electronic Publication: 2026 Jul 04.
Publication Type: Letter
Journal Info: Publisher: Blackwell Science Country of Publication: England NLM ID: 9442916 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1365-2516 (Electronic) Linking ISSN: 13518216 NLM ISO Abbreviation: Haemophilia Subsets: MEDLINE
Database: MEDLINE Ultimate
Description
ISSN:1365-2516
DOI:10.1111/hae.70338