Clinical Outcomes of Efanesoctocog Alfa Prophylaxis in Children With Severe Haemophilia A: Interim Data From XTEND-ed.

Saved in:
Bibliographic Details
Title: Clinical Outcomes of Efanesoctocog Alfa Prophylaxis in Children With Severe Haemophilia A: Interim Data From XTEND-ed.
Authors: Malec L; Versiti Blood Research Institute, Milwaukee, Wisconsin, USA.; Division of Hematology & Oncology, Departments of Medicine and Pediatrics, Medical College of Wisconsin, Milwaukee, Wisconsin, USA., Nolan B; Haematology Department, Children's Health Ireland, Dublin, Ireland., Chan AKC; McMaster Children's Hospital, McMaster University, Hamilton, Ontario, Canada., Albisetti M; University Children's Hospital Zurich, Zurich, Switzerland., Chou SC; Department of Internal Medicine, Division of Hematology, National Taiwan University Hospital, College of Medicine, National Taiwan University, Taipei City, Taiwan., Zulfikar B; Division of Pediatric Hematology-Oncology, Istanbul University Oncology Institute, Istanbul, Türkiye., Simpson M; Rush Hemophilia and Thrombophilia Center, Rush University Medical Center, Chicago, Illinois, USA., Feng L; Sanofi, Shanghai, China., Palmborg H; Sobi, Stockholm, Sweden., Neill G; Sanofi, Cambridge, UK., Abad-Franch L; Sobi, Basel, Switzerland., Gunawardena S; Sanofi, Morristown, New Jersey, USA., Fijnvandraat K; Emma Kinderziekenhuis/AMC, University of Amsterdam, Amsterdam, Netherlands.
Source: Haemophilia : the official journal of the World Federation of Hemophilia [Haemophilia] 2026 Jul 04. Date of Electronic Publication: 2026 Jul 04.
Publication Type: Letter
Journal Info: Publisher: Blackwell Science Country of Publication: England NLM ID: 9442916 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1365-2516 (Electronic) Linking ISSN: 13518216 NLM ISO Abbreviation: Haemophilia Subsets: MEDLINE
Database: MEDLINE Ultimate
FullText Text:
  Availability: 0
Header DbId: mdl
DbLabel: MEDLINE Ultimate
An: 42400392
AccessLevel: 2
PubType: Editorial & Opinion
PubTypeId: editorialOpinion
PreciseRelevancyScore: 0
IllustrationInfo
Items – Name: Title
  Label: Title
  Group: Ti
  Data: Clinical Outcomes of Efanesoctocog Alfa Prophylaxis in Children With Severe Haemophilia A: Interim Data From XTEND-ed.
– Name: Author
  Label: Authors
  Group: Au
  Data: <searchLink fieldCode="AU" term="%22Malec+L%22">Malec L</searchLink>; Versiti Blood Research Institute, Milwaukee, Wisconsin, USA.; Division of Hematology & Oncology, Departments of Medicine and Pediatrics, Medical College of Wisconsin, Milwaukee, Wisconsin, USA.<br /><searchLink fieldCode="AU" term="%22Nolan+B%22">Nolan B</searchLink>; Haematology Department, Children's Health Ireland, Dublin, Ireland.<br /><searchLink fieldCode="AU" term="%22Chan+AKC%22">Chan AKC</searchLink>; McMaster Children's Hospital, McMaster University, Hamilton, Ontario, Canada.<br /><searchLink fieldCode="AU" term="%22Albisetti+M%22">Albisetti M</searchLink>; University Children's Hospital Zurich, Zurich, Switzerland.<br /><searchLink fieldCode="AU" term="%22Chou+SC%22">Chou SC</searchLink>; Department of Internal Medicine, Division of Hematology, National Taiwan University Hospital, College of Medicine, National Taiwan University, Taipei City, Taiwan.<br /><searchLink fieldCode="AU" term="%22Zulfikar+B%22">Zulfikar B</searchLink>; Division of Pediatric Hematology-Oncology, Istanbul University Oncology Institute, Istanbul, Türkiye.<br /><searchLink fieldCode="AU" term="%22Simpson+M%22">Simpson M</searchLink>; Rush Hemophilia and Thrombophilia Center, Rush University Medical Center, Chicago, Illinois, USA.<br /><searchLink fieldCode="AU" term="%22Feng+L%22">Feng L</searchLink>; Sanofi, Shanghai, China.<br /><searchLink fieldCode="AU" term="%22Palmborg+H%22">Palmborg H</searchLink>; Sobi, Stockholm, Sweden.<br /><searchLink fieldCode="AU" term="%22Neill+G%22">Neill G</searchLink>; Sanofi, Cambridge, UK.<br /><searchLink fieldCode="AU" term="%22Abad-Franch+L%22">Abad-Franch L</searchLink>; Sobi, Basel, Switzerland.<br /><searchLink fieldCode="AU" term="%22Gunawardena+S%22">Gunawardena S</searchLink>; Sanofi, Morristown, New Jersey, USA.<br /><searchLink fieldCode="AU" term="%22Fijnvandraat+K%22">Fijnvandraat K</searchLink>; Emma Kinderziekenhuis/AMC, University of Amsterdam, Amsterdam, Netherlands.
– Name: TitleSource
  Label: Source
  Group: Src
  Data: <searchLink fieldCode="JN" term="%229442916%22">Haemophilia : the official journal of the World Federation of Hemophilia</searchLink> [Haemophilia] 2026 Jul 04. <i>Date of Electronic Publication: </i>2026 Jul 04.
– Name: TypePub
  Label: Publication Type
  Group: TypPub
  Data: Letter
– Name: TitleSource
  Label: Journal Info
  Group: Src
  Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Blackwell+Science%22">Blackwell Science </searchLink><i>Country of Publication: </i>England <i>NLM ID: </i>9442916 <i>Publication Model: </i>Print-Electronic <i>Cited Medium: </i>Internet <i>ISSN: </i>1365-2516 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2213518216%22">13518216 </searchLink><i>NLM ISO Abbreviation: </i>Haemophilia <i>Subsets: </i>MEDLINE
PLink https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=mdl&AN=42400392
RecordInfo BibRecord:
  BibEntity:
    Identifiers:
      – Type: doi
        Value: 10.1111/hae.70338
    Languages:
      – Code: eng
        Text: English
    Titles:
      – TitleFull: Clinical Outcomes of Efanesoctocog Alfa Prophylaxis in Children With Severe Haemophilia A: Interim Data From XTEND-ed.
        Type: main
  BibRelationships:
    HasContributorRelationships:
      – PersonEntity:
          Name:
            NameFull: Malec L
      – PersonEntity:
          Name:
            NameFull: Nolan B
      – PersonEntity:
          Name:
            NameFull: Chan AKC
      – PersonEntity:
          Name:
            NameFull: Albisetti M
      – PersonEntity:
          Name:
            NameFull: Chou SC
      – PersonEntity:
          Name:
            NameFull: Zulfikar B
      – PersonEntity:
          Name:
            NameFull: Simpson M
      – PersonEntity:
          Name:
            NameFull: Feng L
      – PersonEntity:
          Name:
            NameFull: Palmborg H
      – PersonEntity:
          Name:
            NameFull: Neill G
      – PersonEntity:
          Name:
            NameFull: Abad-Franch L
      – PersonEntity:
          Name:
            NameFull: Gunawardena S
      – PersonEntity:
          Name:
            NameFull: Fijnvandraat K
    IsPartOfRelationships:
      – BibEntity:
          Dates:
            – D: 04
              M: 07
              Text: 2026 Jul 04
              Type: published
              Y: 2026
          Identifiers:
            – Type: issn-electronic
              Value: 1365-2516
          Titles:
            – TitleFull: Haemophilia : the official journal of the World Federation of Hemophilia
              Type: main
ResultId 1