Clinical Outcomes of Efanesoctocog Alfa Prophylaxis in Children With Severe Haemophilia A: Interim Data From XTEND-ed.
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| Title: | Clinical Outcomes of Efanesoctocog Alfa Prophylaxis in Children With Severe Haemophilia A: Interim Data From XTEND-ed. |
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| Authors: | Malec L; Versiti Blood Research Institute, Milwaukee, Wisconsin, USA.; Division of Hematology & Oncology, Departments of Medicine and Pediatrics, Medical College of Wisconsin, Milwaukee, Wisconsin, USA., Nolan B; Haematology Department, Children's Health Ireland, Dublin, Ireland., Chan AKC; McMaster Children's Hospital, McMaster University, Hamilton, Ontario, Canada., Albisetti M; University Children's Hospital Zurich, Zurich, Switzerland., Chou SC; Department of Internal Medicine, Division of Hematology, National Taiwan University Hospital, College of Medicine, National Taiwan University, Taipei City, Taiwan., Zulfikar B; Division of Pediatric Hematology-Oncology, Istanbul University Oncology Institute, Istanbul, Türkiye., Simpson M; Rush Hemophilia and Thrombophilia Center, Rush University Medical Center, Chicago, Illinois, USA., Feng L; Sanofi, Shanghai, China., Palmborg H; Sobi, Stockholm, Sweden., Neill G; Sanofi, Cambridge, UK., Abad-Franch L; Sobi, Basel, Switzerland., Gunawardena S; Sanofi, Morristown, New Jersey, USA., Fijnvandraat K; Emma Kinderziekenhuis/AMC, University of Amsterdam, Amsterdam, Netherlands. |
| Source: | Haemophilia : the official journal of the World Federation of Hemophilia [Haemophilia] 2026 Jul 04. Date of Electronic Publication: 2026 Jul 04. |
| Publication Type: | Letter |
| Journal Info: | Publisher: Blackwell Science Country of Publication: England NLM ID: 9442916 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1365-2516 (Electronic) Linking ISSN: 13518216 NLM ISO Abbreviation: Haemophilia Subsets: MEDLINE |
| Database: | MEDLINE Ultimate |
| FullText | Text: Availability: 0 |
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| Header | DbId: mdl DbLabel: MEDLINE Ultimate An: 42400392 AccessLevel: 2 PubType: Editorial & Opinion PubTypeId: editorialOpinion PreciseRelevancyScore: 0 |
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| Items | – Name: Title Label: Title Group: Ti Data: Clinical Outcomes of Efanesoctocog Alfa Prophylaxis in Children With Severe Haemophilia A: Interim Data From XTEND-ed. – Name: Author Label: Authors Group: Au Data: <searchLink fieldCode="AU" term="%22Malec+L%22">Malec L</searchLink>; Versiti Blood Research Institute, Milwaukee, Wisconsin, USA.; Division of Hematology & Oncology, Departments of Medicine and Pediatrics, Medical College of Wisconsin, Milwaukee, Wisconsin, USA.<br /><searchLink fieldCode="AU" term="%22Nolan+B%22">Nolan B</searchLink>; Haematology Department, Children's Health Ireland, Dublin, Ireland.<br /><searchLink fieldCode="AU" term="%22Chan+AKC%22">Chan AKC</searchLink>; McMaster Children's Hospital, McMaster University, Hamilton, Ontario, Canada.<br /><searchLink fieldCode="AU" term="%22Albisetti+M%22">Albisetti M</searchLink>; University Children's Hospital Zurich, Zurich, Switzerland.<br /><searchLink fieldCode="AU" term="%22Chou+SC%22">Chou SC</searchLink>; Department of Internal Medicine, Division of Hematology, National Taiwan University Hospital, College of Medicine, National Taiwan University, Taipei City, Taiwan.<br /><searchLink fieldCode="AU" term="%22Zulfikar+B%22">Zulfikar B</searchLink>; Division of Pediatric Hematology-Oncology, Istanbul University Oncology Institute, Istanbul, Türkiye.<br /><searchLink fieldCode="AU" term="%22Simpson+M%22">Simpson M</searchLink>; Rush Hemophilia and Thrombophilia Center, Rush University Medical Center, Chicago, Illinois, USA.<br /><searchLink fieldCode="AU" term="%22Feng+L%22">Feng L</searchLink>; Sanofi, Shanghai, China.<br /><searchLink fieldCode="AU" term="%22Palmborg+H%22">Palmborg H</searchLink>; Sobi, Stockholm, Sweden.<br /><searchLink fieldCode="AU" term="%22Neill+G%22">Neill G</searchLink>; Sanofi, Cambridge, UK.<br /><searchLink fieldCode="AU" term="%22Abad-Franch+L%22">Abad-Franch L</searchLink>; Sobi, Basel, Switzerland.<br /><searchLink fieldCode="AU" term="%22Gunawardena+S%22">Gunawardena S</searchLink>; Sanofi, Morristown, New Jersey, USA.<br /><searchLink fieldCode="AU" term="%22Fijnvandraat+K%22">Fijnvandraat K</searchLink>; Emma Kinderziekenhuis/AMC, University of Amsterdam, Amsterdam, Netherlands. – Name: TitleSource Label: Source Group: Src Data: <searchLink fieldCode="JN" term="%229442916%22">Haemophilia : the official journal of the World Federation of Hemophilia</searchLink> [Haemophilia] 2026 Jul 04. <i>Date of Electronic Publication: </i>2026 Jul 04. – Name: TypePub Label: Publication Type Group: TypPub Data: Letter – Name: TitleSource Label: Journal Info Group: Src Data: <i>Publisher: </i><searchLink fieldCode="PB" term="%22Blackwell+Science%22">Blackwell Science </searchLink><i>Country of Publication: </i>England <i>NLM ID: </i>9442916 <i>Publication Model: </i>Print-Electronic <i>Cited Medium: </i>Internet <i>ISSN: </i>1365-2516 (Electronic) <i>Linking ISSN: </i><searchLink fieldCode="IS" term="%2213518216%22">13518216 </searchLink><i>NLM ISO Abbreviation: </i>Haemophilia <i>Subsets: </i>MEDLINE |
| PLink | https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=mdl&AN=42400392 |
| RecordInfo | BibRecord: BibEntity: Identifiers: – Type: doi Value: 10.1111/hae.70338 Languages: – Code: eng Text: English Titles: – TitleFull: Clinical Outcomes of Efanesoctocog Alfa Prophylaxis in Children With Severe Haemophilia A: Interim Data From XTEND-ed. Type: main BibRelationships: HasContributorRelationships: – PersonEntity: Name: NameFull: Malec L – PersonEntity: Name: NameFull: Nolan B – PersonEntity: Name: NameFull: Chan AKC – PersonEntity: Name: NameFull: Albisetti M – PersonEntity: Name: NameFull: Chou SC – PersonEntity: Name: NameFull: Zulfikar B – PersonEntity: Name: NameFull: Simpson M – PersonEntity: Name: NameFull: Feng L – PersonEntity: Name: NameFull: Palmborg H – PersonEntity: Name: NameFull: Neill G – PersonEntity: Name: NameFull: Abad-Franch L – PersonEntity: Name: NameFull: Gunawardena S – PersonEntity: Name: NameFull: Fijnvandraat K IsPartOfRelationships: – BibEntity: Dates: – D: 04 M: 07 Text: 2026 Jul 04 Type: published Y: 2026 Identifiers: – Type: issn-electronic Value: 1365-2516 Titles: – TitleFull: Haemophilia : the official journal of the World Federation of Hemophilia Type: main |
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