Gene supplementation therapy restores motor deficits in Gnao1[C215Y] mice and proves broad efficacy in C. elegans model.
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| Title: | Gene supplementation therapy restores motor deficits in Gnao1[C215Y] mice and proves broad efficacy in C. elegans model. |
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| Authors: | Cocozza G; Department of Physiology and Pharmacology, Sapienza University of Rome, Rome, Italy., D'Andrea T; IRCCS Neuromed, Pozzilli, Italy., Di Rocco M; Department of Oncology and Molecular Medicine, Istituto Superiore di Sanità, Rome, Italy., Busdraghi LM; Department of Physiology and Pharmacology, Sapienza University of Rome, Rome, Italy., Chilà G; Department of Physiology and Pharmacology, Sapienza University of Rome, Rome, Italy., Lin X; Department of Physiology and Pharmacology, Sapienza University of Rome, Rome, Italy., Lanza E; D-tails, Rome, Italy., Collaud F; Université Paris-Saclay, University Evry, Integrare Research Unit UMR_S951, Inserm, Genethon, Evry, 91000, France.; Genethon, Evry, 91000, France., Follo FC; Department of Oncology and Molecular Medicine, Istituto Superiore di Sanità, Rome, Italy., Buccheri C; National Research Council (Institute of Biochemistry and Cell Biology), Campus International Development (European Mouse Mutant Archive- INFRAFRONTIER), Monterotondo Scalo, Rome, Italy., Folli V; D-tails, Rome, Italy., Ronzitti G; Université Paris-Saclay, University Evry, Integrare Research Unit UMR_S951, Inserm, Genethon, Evry, 91000, France.; Genethon, Evry, 91000, France., Scavizzi F; National Research Council (Institute of Biochemistry and Cell Biology), Campus International Development (European Mouse Mutant Archive- INFRAFRONTIER), Monterotondo Scalo, Rome, Italy., Raspa M; National Research Council (Institute of Biochemistry and Cell Biology), Campus International Development (European Mouse Mutant Archive- INFRAFRONTIER), Monterotondo Scalo, Rome, Italy., Leuzzi V; Department of Human Neuroscience, Sapienza University of Rome, Rome, Italy., Katanaev VL; Department of Cell Physiology and Metabolism, Faculty of Medicine, Translational Research Center in Oncohaematology, University of Geneva, Geneva, 1211, Switzerland.; Qatar Biomedical Research Institute, College of Health and Life Sciences, Hamad Bin Khalifa University, P.O. Box 34110, Doha, Qatar., Galosi S; Department of Human Neuroscience, Sapienza University of Rome, Rome, Italy., Fucile S; Department of Physiology and Pharmacology, Sapienza University of Rome, Rome, Italy.; IRCCS Neuromed, Pozzilli, Italy., Martinelli S; Department of Oncology and Molecular Medicine, Istituto Superiore di Sanità, Rome, Italy., D'Alessandro G; IRCCS Neuromed, Pozzilli, Italy. giuseppina.dalessandro@uniroma1.it.; Laboratory affiliated to Istituto Pasteur Rome, Department of Physiology and Pharmacology, Sapienza University of Rome, Rome, Italy. giuseppina.dalessandro@uniroma1.it., Limatola C; IRCCS Neuromed, Pozzilli, Italy. cristina.limatola@uniroma1.it.; Laboratory affiliated to Istituto Pasteur Rome, Department of Physiology and Pharmacology, Sapienza University of Rome, Rome, Italy. cristina.limatola@uniroma1.it. |
| Source: | Acta neuropathologica communications [Acta Neuropathol Commun] 2026 Jul 21. Date of Electronic Publication: 2026 Jul 21. |
| Publication Type: | Journal Article |
| Journal Info: | Publisher: BioMed Central Country of Publication: England NLM ID: 101610673 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 2051-5960 (Electronic) Linking ISSN: 20515960 NLM ISO Abbreviation: Acta Neuropathol Commun Subsets: MEDLINE |
| Database: | MEDLINE Ultimate |
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