Cardiotoxic Effects and Microdystrophin Expression after Gene Therapy for DMD.

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Bibliographic Details
Title: Cardiotoxic Effects and Microdystrophin Expression after Gene Therapy for DMD.
Authors: Samelson-Jones BJ; Children's Hospital of Philadelphia, Philadelphia., Martos-Rus C; Children's Hospital of Philadelphia, Philadelphia., Yrigollen CM; Children's Hospital of Philadelphia, Philadelphia., Tecedor L; Children's Hospital of Philadelphia, Philadelphia., Small JC; Children's Hospital of Philadelphia, Philadelphia., Matesanz SE; Children's Hospital of Philadelphia, Philadelphia., Watson CT; Children's Hospital of Philadelphia, Philadelphia., Vanden Heuvel AR; Children's Hospital of Philadelphia, Philadelphia., Carrig S; Children's Hospital of Philadelphia, Philadelphia., Yum SW; Children's Hospital of Philadelphia, Philadelphia., Brandsema JF; Children's Hospital of Philadelphia, Philadelphia., Lin K; Children's Hospital of Philadelphia, Philadelphia., Wittlieb-Weber C; Children's Hospital of Philadelphia, Philadelphia., Viaene AN; Children's Hospital of Philadelphia, Philadelphia., Russo PP; Children's Hospital of Philadelphia, Philadelphia., Partington S; University of Pennsylvania, Philadelphia., Huynh K; Children's Hospital of Philadelphia, Philadelphia., Seneviratne T; Children's Hospital of Philadelphia, Philadelphia., Juarez Rojas S; Emory University School of Medicine, Atlanta., Doshi BS; Emory University School of Medicine, Atlanta., Shieh P; David Geffen School of Medicine, University of California, Los Angeles, Los Angeles., Flanigan KM; Nationwide Children's Hospital, Columbus, OH., Frair E; Nationwide Children's Hospital, Columbus, OH., Nicolau S; Nationwide Children's Hospital, Columbus, OH., Lawlor MW; Diverge Translational Science Laboratory, Milwaukee., Crudele JM; University of Washington School of Medicine, Seattle., Davidson BL; Children's Hospital of Philadelphia, Philadelphia., George LA; Children's Hospital of Philadelphia, Philadelphia.
Source: The New England journal of medicine [N Engl J Med] 2026 Aug 06; Vol. 395 (6), pp. 615-617. Date of Electronic Publication: 2026 Jul 22.
Publication Type: Letter
Journal Info: Publisher: Massachusetts Medical Society Country of Publication: United States NLM ID: 0255562 Publication Model: Print-Electronic Cited Medium: Internet ISSN: 1533-4406 (Electronic) Linking ISSN: 00284793 NLM ISO Abbreviation: N Engl J Med Subsets: MEDLINE; In Process
Database: MEDLINE Ultimate
Description
ISSN:1533-4406
DOI:10.1056/NEJMc2518477