Gene therapy for Crigler Najjar syndrome: results of the dose finding part of the CareCN, phase 1-2 clinical trial.

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Bibliographic Details
Title: Gene therapy for Crigler Najjar syndrome: results of the dose finding part of the CareCN, phase 1-2 clinical trial.
Authors: D'Antiga, L., Beuers, U., Brunetti-Pierri, N., Baumann, U., Di Giorgio, A., Aronson, S., Hubert, A., Romano, R., Junge, N., Bosma, P., Bortolussi, G., Muro, A. F., Pavlyuk, M., Veron, P., Ronzitti, G., Collaud, F., Knuchel-Legendre, N., Mingozzi, F., Labrune, P.
Source: Journal of pediatric gastroenterology and nutrition 2022 Supplement; Vol. 74.
Journal Info: Publisher: Wiley-Blackwell ISSN: 0277-2116
Database: MEDLINE Ultimate
Description
ISSN:1536-4801
DOI:10.1097/MPG.0000000000003446