Combination therapy (eliglustat + velaglucerase alfa) in a pediatric patient with Gaucher disease type 1 and hereditary spherocytosis.

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Bibliographic Details
Title: Combination therapy (eliglustat + velaglucerase alfa) in a pediatric patient with Gaucher disease type 1 and hereditary spherocytosis.
Authors: Bailey, Laurie1, Ambruso, Daniel2, Grabowski, Gregory1, Burrow, Thomas A.1
Source: Molecular Genetics & Metabolism. Feb2015, Vol. 114 Issue 2, pS17-S17. 1p.
Database: Academic Search Ultimate
Description
ISSN:10967192
DOI:10.1016/j.ymgme.2014.12.020