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G.O.20 - Reveglucosidase alfa (BMN 701), a GILT-tagged recombinant human acid alpha glucosidase (rhGAA), evaluation in late-onset Pompe disease: Preliminary clinical efficacy and safety results of an extension study (72-week results).

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Bibliographic Details
Title: G.O.20 - Reveglucosidase alfa (BMN 701), a GILT-tagged recombinant human acid alpha glucosidase (rhGAA), evaluation in late-onset Pompe disease: Preliminary clinical efficacy and safety results of an extension study (72-week results).
Authors: Hiwot, T.1, Barohn, R.2, Bratkovic, D.3, Byrne, B.4, Desnuelle, C.5, Hughes, D.6, Laforêt, P.7, Mengel, E.8, Roberts, M.9, Yang, K.10, Heusner, C.10, Dummer, W.10
Source: Neuromuscular Disorders. Oct2015 Supplement 2, Vol. 25, pS313-S314. 1p.
Database: Academic Search Ultimate
Description
ISSN:09608966
DOI:10.1016/j.nmd.2015.06.453