Treatment of Fabry's Disease with the Pharmacologic Chaperone Migalastat.

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Bibliographic Details
Title: Treatment of Fabry's Disease with the Pharmacologic Chaperone Migalastat.
Authors: Germain, D. P.1,2 dominique.germain@uvsq.fr, Hughes, D. A.3, Nicholls, K.4, Bichet, D. G.5, Giugliani, R.6, Wilcox, W. R.7, Feliciani, C.8, Shankar, S. P.7,9, Ezgu, F.10, Amartino, H.11, Bratkovic, D.12, Feldt-Rasmussen, U.13, Nedd, K.14, El Din, U. Sharaf15, Lourenco, C. M.16, Banikazemi, M.17, Charrow, J.18,19, Dasouki, M.20, Finegold, D.21, Giraldo, P.22
Source: New England Journal of Medicine. 8/11/2016, Vol. 375 Issue 6, p545-555. 11p.
Database: Academic Search Ultimate
Description
ISSN:00284793
DOI:10.1056/NEJMoa1510198