Cognitive and academic outcomes in long-term survivors of infantile-onset Pompe disease: A longitudinal follow-up.
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| Title: | Cognitive and academic outcomes in long-term survivors of infantile-onset Pompe disease: A longitudinal follow-up. |
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| Authors: | Spiridigliozzi, Gail A.1 gail.spiridigliozzi@duke.edu, Keeling, Lori A.2 lori.keeling@duke.edu, Stefanescu, Mihaela3 mihaela.stefanescu@duke.edu, Li, Cindy3 cindy.li1@duke.edu, Austin, Stephanie3 stephanie.austin@duke.edu, Kishnani, Priya S.3 priya.kishnani@duke.edu |
| Source: | Molecular Genetics & Metabolism. Jun2017, Vol. 121 Issue 2, p127-137. 11p. |
| Database: | Academic Search Ultimate |
| ISSN: | 10967192 |
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| DOI: | 10.1016/j.ymgme.2017.04.014 |