P.373 - AVXS-101 phase 1 gene therapy clinical trial in SMA Type 1: decreased need of ventilatory and nutritional support at End-of-Study.

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Bibliographic Details
Title: P.373 - AVXS-101 phase 1 gene therapy clinical trial in SMA Type 1: decreased need of ventilatory and nutritional support at End-of-Study.
Authors: Shell, R.1, Al-Zaidy, S.1, Arnold, W.2, Rodino-Klapac, L.1, Prior, T.2, Lowes, L.1, Alfano, L.1, Berry, K.1, Church, K.1, Kissel, J.2, Nagendran, S.3, L'italien, J.3, Sproule, D.3, Wells, C.3, Burghes, A.2, Foust, K.3, Meyer, K.1, Likhite, S.1, Kaspar, B.1, Mendell, J.1
Source: Neuromuscular Disorders. Oct2017 Supplement 2, Vol. 27, pS208-S208. 1p.
Database: Academic Search Ultimate
Description
ISSN:09608966
DOI:10.1016/j.nmd.2017.06.413