Amphiphilic lipopeptide significantly enhances uptake of charge-neutral splice switching morpholino oligonucleotide in spinal muscular atrophy patient-derived fibroblasts.

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Bibliographic Details
Title: Amphiphilic lipopeptide significantly enhances uptake of charge-neutral splice switching morpholino oligonucleotide in spinal muscular atrophy patient-derived fibroblasts.
Authors: Tajik-Ahmadabad, Behnoosh1, Polyzos, Anastasios1,2, Separovic, Frances1, Shabanpoor, Fazel3 Fazel.shabanpoor@unimelb.edu.au
Source: International Journal of Pharmaceutics. Oct2017, Vol. 532 Issue 1, p21-28. 8p.
Database: Academic Search Ultimate
Description
ISSN:03785173
DOI:10.1016/j.ijpharm.2017.08.116