Amphiphilic lipopeptide significantly enhances uptake of charge-neutral splice switching morpholino oligonucleotide in spinal muscular atrophy patient-derived fibroblasts.
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| Title: | Amphiphilic lipopeptide significantly enhances uptake of charge-neutral splice switching morpholino oligonucleotide in spinal muscular atrophy patient-derived fibroblasts. |
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| Authors: | Tajik-Ahmadabad, Behnoosh1, Polyzos, Anastasios1,2, Separovic, Frances1, Shabanpoor, Fazel3 Fazel.shabanpoor@unimelb.edu.au |
| Source: | International Journal of Pharmaceutics. Oct2017, Vol. 532 Issue 1, p21-28. 8p. |
| Database: | Academic Search Ultimate |
| ISSN: | 03785173 |
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| DOI: | 10.1016/j.ijpharm.2017.08.116 |