Patient reported outcomes in MPS IVA patients receiving enzyme replacement therapy.

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Bibliographic Details
Title: Patient reported outcomes in MPS IVA patients receiving enzyme replacement therapy.
Authors: Adam, Jacqueline1, Morrison, Alexandra1, Wiseman, Samantha1
Source: Molecular Genetics & Metabolism. Feb2019, Vol. 126 Issue 2, pS19-S19. 1p.
Database: Academic Search Ultimate
Description
ISSN:10967192
DOI:10.1016/j.ymgme.2018.12.023