PRO125 SUITABILITY OF NATURAL HISTORY DATA FOR EXTERNAL CONTROLS IN DUCHENNE MUSCULAR DYSTROPHY.
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| Title: | PRO125 SUITABILITY OF NATURAL HISTORY DATA FOR EXTERNAL CONTROLS IN DUCHENNE MUSCULAR DYSTROPHY. |
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| Authors: | Goemans, N.1 (AUTHOR), Wong, B.2 (AUTHOR), Muntoni, F.3 (AUTHOR), McDonald, C.4 (AUTHOR), Mercuri, E.5 (AUTHOR), Manzur, A.3 (AUTHOR), Signorovitch, J.6 (AUTHOR), Sajeev, G.6 (AUTHOR), Wong, H.6 (AUTHOR), Hossain, I.6 (AUTHOR), Jenkins, M.7 (AUTHOR), Ward, S.J.8 (AUTHOR) |
| Source: | Value in Health. 2019 Supplement 3, Vol. 22, pS864-S864. 1p. |
| Database: | Academic Search Ultimate |
| ISSN: | 10983015 |
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| DOI: | 10.1016/j.jval.2019.09.2455 |