Assessing Preferences for Rare Disease Treatment: Qualitative Development of the Paroxysmal Nocturnal Hemoglobinuria Patient Preference Questionnaire (PNH-PPQ©).

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Title: Assessing Preferences for Rare Disease Treatment: Qualitative Development of the Paroxysmal Nocturnal Hemoglobinuria Patient Preference Questionnaire (PNH-PPQ©).
Authors: Kaiser, Karen (AUTHOR), Yount, Susan E (AUTHOR), Martens, Christa E (AUTHOR), Webster, Kimberly A (AUTHOR), Shaunfield, Sara (AUTHOR), Sparling, Amy (AUTHOR), Peipert, John Devin (AUTHOR), Cella, David (AUTHOR), Rottinghaus, Scott T (AUTHOR), Donato, Bonnie MK (AUTHOR), Wells, Richard (AUTHOR), Tomazos, Ioannis (AUTHOR)
Source: Patient Preference & Adherence. Apr2020, Vol. 14, p705-715. 11p.
Database: Academic Search Ultimate
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ISSN:1177889X
DOI:10.2147/PPA.S233830