Standardising clinical outcomes measures for adult clinical trials in Fabry disease: A global Delphi consensus.
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| Title: | Standardising clinical outcomes measures for adult clinical trials in Fabry disease: A global Delphi consensus. |
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| Authors: | Moreno-Martinez, D.1 (AUTHOR), Aguiar, P.2 (AUTHOR), Auray-Blais, C.3 (AUTHOR), Beck, M.4 (AUTHOR), Bichet, D.G.5 (AUTHOR), Burlina, A.6 (AUTHOR), Cole, D.7 (AUTHOR), Elliott, P.8 (AUTHOR), Feldt-Rasmussen, U.9 (AUTHOR), Feriozzi, S.10 (AUTHOR), Fletcher, J.11 (AUTHOR), Giugliani, R.12 (AUTHOR), Jovanovic, A.13 (AUTHOR), Kampmann, C.14 (AUTHOR), Langeveld, M.15 (AUTHOR), Lidove, O.16 (AUTHOR), Linhart, A.17 (AUTHOR), Mauer, M.18 (AUTHOR), Moon, J.C.19 (AUTHOR), Muir, A.20 (AUTHOR) |
| Source: | Molecular Genetics & Metabolism. Apr2021, Vol. 132 Issue 4, p234-243. 10p. |
| Database: | Academic Search Ultimate |
| ISSN: | 10967192 |
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| DOI: | 10.1016/j.ymgme.2021.02.001 |