In vivo genome editing in mouse restores dystrophin expression in Duchenne muscular dystrophy patient muscle fibers.

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Bibliographic Details
Title: In vivo genome editing in mouse restores dystrophin expression in Duchenne muscular dystrophy patient muscle fibers.
Authors: Chen, Menglong1 (AUTHOR), Shi, Hui2,3 (AUTHOR), Gou, Shixue2,3 (AUTHOR), Wang, Xiaomin2,3 (AUTHOR), Li, Lei2,3 (AUTHOR), Jin, Qin2,3 (AUTHOR), Wu, Han2 (AUTHOR), Zhang, Huili4 (AUTHOR), Li, Yaqin5 (AUTHOR), Wang, Liang1 (AUTHOR), Li, Huan1 (AUTHOR), Lin, Jinfu1 (AUTHOR), Guo, Wenjing6 (AUTHOR), Jiang, Zhiwu2 (AUTHOR), Yang, Xiaoyu7 (AUTHOR), Xu, Anding8 (AUTHOR), Zhu, Yuling1 (AUTHOR), Zhang, Cheng1 (AUTHOR) Zhangch6@mail.sysu.edu.cn, Lai, Liangxue2,9,10,11 (AUTHOR) lai_liangxue@gibh.ac.cn, Li, Xiaoping2,12 (AUTHOR) lixiaoping@mail.sysu.edu.cn
Source: Genome Medicine. 4/12/2021, Vol. 13 Issue 1, p1-19. 19p.
Database: Academic Search Ultimate
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ISSN:1756994X
DOI:10.1186/s13073-021-00876-0