In vivo genome editing in mouse restores dystrophin expression in Duchenne muscular dystrophy patient muscle fibers.
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| Title: | In vivo genome editing in mouse restores dystrophin expression in Duchenne muscular dystrophy patient muscle fibers. |
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| Authors: | Chen, Menglong1 (AUTHOR), Shi, Hui2,3 (AUTHOR), Gou, Shixue2,3 (AUTHOR), Wang, Xiaomin2,3 (AUTHOR), Li, Lei2,3 (AUTHOR), Jin, Qin2,3 (AUTHOR), Wu, Han2 (AUTHOR), Zhang, Huili4 (AUTHOR), Li, Yaqin5 (AUTHOR), Wang, Liang1 (AUTHOR), Li, Huan1 (AUTHOR), Lin, Jinfu1 (AUTHOR), Guo, Wenjing6 (AUTHOR), Jiang, Zhiwu2 (AUTHOR), Yang, Xiaoyu7 (AUTHOR), Xu, Anding8 (AUTHOR), Zhu, Yuling1 (AUTHOR), Zhang, Cheng1 (AUTHOR) Zhangch6@mail.sysu.edu.cn, Lai, Liangxue2,9,10,11 (AUTHOR) lai_liangxue@gibh.ac.cn, Li, Xiaoping2,12 (AUTHOR) lixiaoping@mail.sysu.edu.cn |
| Source: | Genome Medicine. 4/12/2021, Vol. 13 Issue 1, p1-19. 19p. |
| Database: | Academic Search Ultimate |
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| ISSN: | 1756994X |
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| DOI: | 10.1186/s13073-021-00876-0 |