Substrate reduction therapy for Krabbe disease and metachromatic leukodystrophy using a novel ceramide galactosyltransferase inhibitor.
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| Title: | Substrate reduction therapy for Krabbe disease and metachromatic leukodystrophy using a novel ceramide galactosyltransferase inhibitor. |
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| Authors: | Babcock, Michael C.1, Mikulka, Christina R.2, Wang, Bing1, Chandriani, Sanjay1, Chandra, Sundeep1, Xu, Yue1, Webster, Katherine1, Feng, Ying1, Nelvagal, Hemanth R.3, Giaramita, Alex1, Yip, Bryan K.1, Lo, Melanie1, Jiang, Xuntian2, Chao, Qi1, Woloszynek, Josh C.1, Shen, Yuqiao1, Bhagwat, Shripad1, Sands, Mark S.2,4, Crawford, Brett E.1 bcrawford@bmrn.com |
| Source: | Scientific Reports. 7/14/2021, Vol. 11 Issue 1, p1-17. 17p. |
| Database: | Academic Search Ultimate |
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| ISSN: | 20452322 |
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| DOI: | 10.1038/s41598-021-93601-1 |