Substrate reduction therapy for Krabbe disease and metachromatic leukodystrophy using a novel ceramide galactosyltransferase inhibitor.

Saved in:
Bibliographic Details
Title: Substrate reduction therapy for Krabbe disease and metachromatic leukodystrophy using a novel ceramide galactosyltransferase inhibitor.
Authors: Babcock, Michael C.1, Mikulka, Christina R.2, Wang, Bing1, Chandriani, Sanjay1, Chandra, Sundeep1, Xu, Yue1, Webster, Katherine1, Feng, Ying1, Nelvagal, Hemanth R.3, Giaramita, Alex1, Yip, Bryan K.1, Lo, Melanie1, Jiang, Xuntian2, Chao, Qi1, Woloszynek, Josh C.1, Shen, Yuqiao1, Bhagwat, Shripad1, Sands, Mark S.2,4, Crawford, Brett E.1 bcrawford@bmrn.com
Source: Scientific Reports. 7/14/2021, Vol. 11 Issue 1, p1-17. 17p.
Database: Academic Search Ultimate
Full text is not displayed to guests.
Description
ISSN:20452322
DOI:10.1038/s41598-021-93601-1