Liver-directed neonatal gene therapy prevents cardiac, bone, ear, and eye disease in mucopolysaccharidosis I mice

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Title: Liver-directed neonatal gene therapy prevents cardiac, bone, ear, and eye disease in mucopolysaccharidosis I mice
Authors: Liu, Yuli1, Xu, Lingfei1, Hennig, Anne K.1, Kovacs, Attila1, Fu, Annabel1, Chung, Sarah1, Lee, David1, Wang, Bin1, Herati, Ramin S.1, Mosinger Ogilvie, Judith2, Cai, Shi-Rong1, Parker Ponder, Katherine1,3 kponder@im.wustl.edu
Source: Molecular Therapy. Jan2005, Vol. 11 Issue 1, p35-47. 13p.
Database: Academic Search Ultimate
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  Data: Liver-directed neonatal gene therapy prevents cardiac, bone, ear, and eye disease in mucopolysaccharidosis I mice
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  Data: <searchLink fieldCode="AR" term="%22Liu%2C+Yuli%22">Liu, Yuli</searchLink><relatesTo>1</relatesTo><br /><searchLink fieldCode="AR" term="%22Xu%2C+Lingfei%22">Xu, Lingfei</searchLink><relatesTo>1</relatesTo><br /><searchLink fieldCode="AR" term="%22Hennig%2C+Anne+K%2E%22">Hennig, Anne K.</searchLink><relatesTo>1</relatesTo><br /><searchLink fieldCode="AR" term="%22Kovacs%2C+Attila%22">Kovacs, Attila</searchLink><relatesTo>1</relatesTo><br /><searchLink fieldCode="AR" term="%22Fu%2C+Annabel%22">Fu, Annabel</searchLink><relatesTo>1</relatesTo><br /><searchLink fieldCode="AR" term="%22Chung%2C+Sarah%22">Chung, Sarah</searchLink><relatesTo>1</relatesTo><br /><searchLink fieldCode="AR" term="%22Lee%2C+David%22">Lee, David</searchLink><relatesTo>1</relatesTo><br /><searchLink fieldCode="AR" term="%22Wang%2C+Bin%22">Wang, Bin</searchLink><relatesTo>1</relatesTo><br /><searchLink fieldCode="AR" term="%22Herati%2C+Ramin+S%2E%22">Herati, Ramin S.</searchLink><relatesTo>1</relatesTo><br /><searchLink fieldCode="AR" term="%22Mosinger+Ogilvie%2C+Judith%22">Mosinger Ogilvie, Judith</searchLink><relatesTo>2</relatesTo><br /><searchLink fieldCode="AR" term="%22Cai%2C+Shi-Rong%22">Cai, Shi-Rong</searchLink><relatesTo>1</relatesTo><br /><searchLink fieldCode="AR" term="%22Parker+Ponder%2C+Katherine%22">Parker Ponder, Katherine</searchLink><relatesTo>1,3</relatesTo><i> kponder@im.wustl.edu</i>
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  Data: <searchLink fieldCode="JN" term="%22Molecular+Therapy%22">Molecular Therapy</searchLink>. Jan2005, Vol. 11 Issue 1, p35-47. 13p.
PLink https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=asn&AN=15789883
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        Value: 10.1016/j.ymthe.2004.08.027
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              Text: Jan2005
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              Y: 2005
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