Liver-directed neonatal gene therapy prevents cardiac, bone, ear, and eye disease in mucopolysaccharidosis I mice
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| Title: | Liver-directed neonatal gene therapy prevents cardiac, bone, ear, and eye disease in mucopolysaccharidosis I mice |
|---|---|
| Authors: | Liu, Yuli1, Xu, Lingfei1, Hennig, Anne K.1, Kovacs, Attila1, Fu, Annabel1, Chung, Sarah1, Lee, David1, Wang, Bin1, Herati, Ramin S.1, Mosinger Ogilvie, Judith2, Cai, Shi-Rong1, Parker Ponder, Katherine1,3 kponder@im.wustl.edu |
| Source: | Molecular Therapy. Jan2005, Vol. 11 Issue 1, p35-47. 13p. |
| Database: | Academic Search Ultimate |
| FullText | Text: Availability: 0 |
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| Header | DbId: asn DbLabel: Academic Search Ultimate An: 15789883 AccessLevel: 2 PubType: Academic Journal PubTypeId: academicJournal PreciseRelevancyScore: 0 |
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| PLink | https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=asn&AN=15789883 |
| RecordInfo | BibRecord: BibEntity: Identifiers: – Type: doi Value: 10.1016/j.ymthe.2004.08.027 Languages: – Code: eng Text: English PhysicalDescription: Pagination: PageCount: 13 StartPage: 35 Titles: – TitleFull: Liver-directed neonatal gene therapy prevents cardiac, bone, ear, and eye disease in mucopolysaccharidosis I mice Type: main BibRelationships: HasContributorRelationships: – PersonEntity: Name: NameFull: Liu, Yuli – PersonEntity: Name: NameFull: Xu, Lingfei – PersonEntity: Name: NameFull: Hennig, Anne K. – PersonEntity: Name: NameFull: Kovacs, Attila – PersonEntity: Name: NameFull: Fu, Annabel – PersonEntity: Name: NameFull: Chung, Sarah – PersonEntity: Name: NameFull: Lee, David – PersonEntity: Name: NameFull: Wang, Bin – PersonEntity: Name: NameFull: Herati, Ramin S. – PersonEntity: Name: NameFull: Mosinger Ogilvie, Judith – PersonEntity: Name: NameFull: Cai, Shi-Rong – PersonEntity: Name: NameFull: Parker Ponder, Katherine IsPartOfRelationships: – BibEntity: Dates: – D: 01 M: 01 Text: Jan2005 Type: published Y: 2005 Identifiers: – Type: issn-print Value: 15250016 Numbering: – Type: volume Value: 11 – Type: issue Value: 1 Titles: – TitleFull: Molecular Therapy Type: main |
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