Liver-directed neonatal gene therapy prevents cardiac, bone, ear, and eye disease in mucopolysaccharidosis I mice

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Bibliographic Details
Title: Liver-directed neonatal gene therapy prevents cardiac, bone, ear, and eye disease in mucopolysaccharidosis I mice
Authors: Liu, Yuli1, Xu, Lingfei1, Hennig, Anne K.1, Kovacs, Attila1, Fu, Annabel1, Chung, Sarah1, Lee, David1, Wang, Bin1, Herati, Ramin S.1, Mosinger Ogilvie, Judith2, Cai, Shi-Rong1, Parker Ponder, Katherine1,3 kponder@im.wustl.edu
Source: Molecular Therapy. Jan2005, Vol. 11 Issue 1, p35-47. 13p.
Database: Academic Search Ultimate
Description
ISSN:15250016
DOI:10.1016/j.ymthe.2004.08.027