Stakeholders' views on drug development: the congenital disorders of glycosylation community perspective.
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| Title: | Stakeholders' views on drug development: the congenital disorders of glycosylation community perspective. |
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| Authors: | Monticelli, Maria1,2 (AUTHOR), Francisco, Rita2,3,4 (AUTHOR) rab.francisco@campus.fct.unl.pt, Brasil, Sandra2,3,4,5 (AUTHOR), Marques-da-Silva, Dorinda2,5,6,7 (AUTHOR), Rijoff, Tatiana2,8 (AUTHOR), Pascoal, Carlota2,3,4,5 (AUTHOR), Jaeken, Jaak2,9 (AUTHOR), Videira, Paula A.2,3,4,5 (AUTHOR), dos Reis Ferreira, Vanessa2,3,5 (AUTHOR) sindromecdg@gmail.com |
| Source: | Orphanet Journal of Rare Diseases. 7/30/2022, Vol. 17 Issue 1, p1-16. 16p. |
| Database: | Academic Search Ultimate |
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| ISSN: | 17501172 |
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| DOI: | 10.1186/s13023-022-02460-0 |