Improved upper limb function in non-ambulant children with SMA type 2 and 3 during nusinersen treatment: a prospective 3-years SMArtCARE registry study.
Saved in:
| Title: | Improved upper limb function in non-ambulant children with SMA type 2 and 3 during nusinersen treatment: a prospective 3-years SMArtCARE registry study. |
|---|---|
| Authors: | Pechmann, Astrid1 (AUTHOR) astrid.pechmann@uniklinik-freiburg.de, Behrens, Max2 (AUTHOR), Dörnbrack, Katharina3 (AUTHOR), Tassoni, Adrian3 (AUTHOR), Wenzel, Franziska3 (AUTHOR), Stein, Sabine1 (AUTHOR), Vogt, Sibylle1 (AUTHOR), Zöller, Daniela2 (AUTHOR), Bernert, Günther4 (AUTHOR), Hagenacker, Tim5 (AUTHOR), Schara-Schmidt, Ulrike6 (AUTHOR), Walter, Maggie C.7 (AUTHOR), Bertsche, Astrid8 (AUTHOR), Vill, Katharina9 (AUTHOR), Baumann, Matthias10 (AUTHOR), Baumgartner, Manuela11 (AUTHOR), Cordts, Isabell12 (AUTHOR), Eisenkölbl, Astrid13 (AUTHOR), Flotats-Bastardas, Marina14 (AUTHOR), Friese, Johannes15 (AUTHOR) |
| Source: | Orphanet Journal of Rare Diseases. 10/23/2022, Vol. 17 Issue 1, p1-10. 10p. |
| Database: | Academic Search Ultimate |
|
Full text is not displayed to guests.
Login for full access.
|
|
| ISSN: | 17501172 |
|---|---|
| DOI: | 10.1186/s13023-022-02547-8 |