Improved upper limb function in non-ambulant children with SMA type 2 and 3 during nusinersen treatment: a prospective 3-years SMArtCARE registry study.
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| Title: | Improved upper limb function in non-ambulant children with SMA type 2 and 3 during nusinersen treatment: a prospective 3-years SMArtCARE registry study. |
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| Authors: | Pechmann, Astrid1 (AUTHOR) astrid.pechmann@uniklinik-freiburg.de, Behrens, Max2 (AUTHOR), Dörnbrack, Katharina3 (AUTHOR), Tassoni, Adrian3 (AUTHOR), Wenzel, Franziska3 (AUTHOR), Stein, Sabine1 (AUTHOR), Vogt, Sibylle1 (AUTHOR), Zöller, Daniela2 (AUTHOR), Bernert, Günther4 (AUTHOR), Hagenacker, Tim5 (AUTHOR), Schara-Schmidt, Ulrike6 (AUTHOR), Walter, Maggie C.7 (AUTHOR), Bertsche, Astrid8 (AUTHOR), Vill, Katharina9 (AUTHOR), Baumann, Matthias10 (AUTHOR), Baumgartner, Manuela11 (AUTHOR), Cordts, Isabell12 (AUTHOR), Eisenkölbl, Astrid13 (AUTHOR), Flotats-Bastardas, Marina14 (AUTHOR), Friese, Johannes15 (AUTHOR) |
| Source: | Orphanet Journal of Rare Diseases. 10/23/2022, Vol. 17 Issue 1, p1-10. 10p. |
| Database: | Academic Search Ultimate |
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| Header | DbId: asn DbLabel: Academic Search Ultimate An: 159838570 AccessLevel: 2 PubType: Academic Journal PubTypeId: academicJournal PreciseRelevancyScore: 0 |
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| Items | – Name: Title Label: Title Group: Ti Data: Improved upper limb function in non-ambulant children with SMA type 2 and 3 during nusinersen treatment: a prospective 3-years SMArtCARE registry study. – Name: Author Label: Authors Group: Au Data: <searchLink fieldCode="AR" term="%22Pechmann%2C+Astrid%22">Pechmann, Astrid</searchLink><relatesTo>1</relatesTo> (AUTHOR)<i> astrid.pechmann@uniklinik-freiburg.de</i><br /><searchLink fieldCode="AR" term="%22Behrens%2C+Max%22">Behrens, Max</searchLink><relatesTo>2</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Dörnbrack%2C+Katharina%22">Dörnbrack, Katharina</searchLink><relatesTo>3</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Tassoni%2C+Adrian%22">Tassoni, Adrian</searchLink><relatesTo>3</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Wenzel%2C+Franziska%22">Wenzel, Franziska</searchLink><relatesTo>3</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Stein%2C+Sabine%22">Stein, Sabine</searchLink><relatesTo>1</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Vogt%2C+Sibylle%22">Vogt, Sibylle</searchLink><relatesTo>1</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Zöller%2C+Daniela%22">Zöller, Daniela</searchLink><relatesTo>2</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Bernert%2C+Günther%22">Bernert, Günther</searchLink><relatesTo>4</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Hagenacker%2C+Tim%22">Hagenacker, Tim</searchLink><relatesTo>5</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Schara-Schmidt%2C+Ulrike%22">Schara-Schmidt, Ulrike</searchLink><relatesTo>6</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Walter%2C+Maggie+C%2E%22">Walter, Maggie C.</searchLink><relatesTo>7</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Bertsche%2C+Astrid%22">Bertsche, Astrid</searchLink><relatesTo>8</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Vill%2C+Katharina%22">Vill, Katharina</searchLink><relatesTo>9</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Baumann%2C+Matthias%22">Baumann, Matthias</searchLink><relatesTo>10</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Baumgartner%2C+Manuela%22">Baumgartner, Manuela</searchLink><relatesTo>11</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Cordts%2C+Isabell%22">Cordts, Isabell</searchLink><relatesTo>12</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Eisenkölbl%2C+Astrid%22">Eisenkölbl, Astrid</searchLink><relatesTo>13</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Flotats-Bastardas%2C+Marina%22">Flotats-Bastardas, Marina</searchLink><relatesTo>14</relatesTo> (AUTHOR)<br /><searchLink fieldCode="AR" term="%22Friese%2C+Johannes%22">Friese, Johannes</searchLink><relatesTo>15</relatesTo> (AUTHOR) – Name: TitleSource Label: Source Group: Src Data: <searchLink fieldCode="JN" term="%22Orphanet+Journal+of+Rare+Diseases%22">Orphanet Journal of Rare Diseases</searchLink>. 10/23/2022, Vol. 17 Issue 1, p1-10. 10p. |
| PLink | https://search.ebscohost.com/login.aspx?direct=true&site=eds-live&db=asn&AN=159838570 |
| RecordInfo | BibRecord: BibEntity: Identifiers: – Type: doi Value: 10.1186/s13023-022-02547-8 Languages: – Code: eng Text: English PhysicalDescription: Pagination: PageCount: 10 StartPage: 1 Titles: – TitleFull: Improved upper limb function in non-ambulant children with SMA type 2 and 3 during nusinersen treatment: a prospective 3-years SMArtCARE registry study. Type: main BibRelationships: HasContributorRelationships: – PersonEntity: Name: NameFull: Pechmann, Astrid – PersonEntity: Name: NameFull: Behrens, Max – PersonEntity: Name: NameFull: Dörnbrack, Katharina – PersonEntity: Name: NameFull: Tassoni, Adrian – PersonEntity: Name: NameFull: Wenzel, Franziska – PersonEntity: Name: NameFull: Stein, Sabine – PersonEntity: Name: NameFull: Vogt, Sibylle – PersonEntity: Name: NameFull: Zöller, Daniela – PersonEntity: Name: NameFull: Bernert, Günther – PersonEntity: Name: NameFull: Hagenacker, Tim – PersonEntity: Name: NameFull: Schara-Schmidt, Ulrike – PersonEntity: Name: NameFull: Walter, Maggie C. – PersonEntity: Name: NameFull: Bertsche, Astrid – PersonEntity: Name: NameFull: Vill, Katharina – PersonEntity: Name: NameFull: Baumann, Matthias – PersonEntity: Name: NameFull: Baumgartner, Manuela – PersonEntity: Name: NameFull: Cordts, Isabell – PersonEntity: Name: NameFull: Eisenkölbl, Astrid – PersonEntity: Name: NameFull: Flotats-Bastardas, Marina – PersonEntity: Name: NameFull: Friese, Johannes IsPartOfRelationships: – BibEntity: Dates: – D: 23 M: 10 Text: 10/23/2022 Type: published Y: 2022 Identifiers: – Type: issn-print Value: 17501172 Numbering: – Type: volume Value: 17 – Type: issue Value: 1 Titles: – TitleFull: Orphanet Journal of Rare Diseases Type: main |
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