PCR27 Pediatric Outcomes Data Collection Instrument (PODCI) Assessment of Ambulatory Boys Treated With Fordadistrogene Movaparvovec (PF-06939926) for Duchenne Muscular Dystrophy (DMD).

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Bibliographic Details
Title: PCR27 Pediatric Outcomes Data Collection Instrument (PODCI) Assessment of Ambulatory Boys Treated With Fordadistrogene Movaparvovec (PF-06939926) for Duchenne Muscular Dystrophy (DMD).
Authors: Dorling, P1 (AUTHOR), Ryan, K2 (AUTHOR), Posner, NW2 (AUTHOR), Merla, V2 (AUTHOR), Mahn, M2 (AUTHOR), Yong, FH2 (AUTHOR)
Source: Value in Health. 2022 Suppl, Vol. 25 Issue 12, pS395-S395. 1p.
Database: Academic Search Ultimate
Description
ISSN:10983015
DOI:10.1016/j.jval.2022.09.1962