PCR27 Pediatric Outcomes Data Collection Instrument (PODCI) Assessment of Ambulatory Boys Treated With Fordadistrogene Movaparvovec (PF-06939926) for Duchenne Muscular Dystrophy (DMD).
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| Title: | PCR27 Pediatric Outcomes Data Collection Instrument (PODCI) Assessment of Ambulatory Boys Treated With Fordadistrogene Movaparvovec (PF-06939926) for Duchenne Muscular Dystrophy (DMD). |
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| Authors: | Dorling, P1 (AUTHOR), Ryan, K2 (AUTHOR), Posner, NW2 (AUTHOR), Merla, V2 (AUTHOR), Mahn, M2 (AUTHOR), Yong, FH2 (AUTHOR) |
| Source: | Value in Health. 2022 Suppl, Vol. 25 Issue 12, pS395-S395. 1p. |
| Database: | Academic Search Ultimate |
| ISSN: | 10983015 |
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| DOI: | 10.1016/j.jval.2022.09.1962 |