Systematic gene therapy derived from an investigative study of AAV2/8 vector gene therapy for Fabry disease.

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Bibliographic Details
Title: Systematic gene therapy derived from an investigative study of AAV2/8 vector gene therapy for Fabry disease.
Authors: Deng, Mulan1 (AUTHOR), Zhou, Hongyu1 (AUTHOR), He, Shaomei1 (AUTHOR), Qiu, Haoheng1 (AUTHOR), Wang, Yanping1 (AUTHOR), Zhao, April Yuanyi1 (AUTHOR), Mu, Yunping1 (AUTHOR) muyunping2018@gdut.edu.cn, Li, Fanghong1 (AUTHOR) fli@gdut.edu.cn, Zhao, Allan Zijian1 (AUTHOR) azzhao@gdut.edu.cn
Source: Orphanet Journal of Rare Diseases. 9/5/2023, Vol. 18 Issue 1, p1-13. 13p.
Database: Academic Search Ultimate
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ISSN:17501172
DOI:10.1186/s13023-023-02894-0