VP55 Topline data analysis of the phase 1/2 clinical trial evaluating AOC 1001 in adult patients with myotonic dystrophy type 1: MARINA.

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Bibliographic Details
Title: VP55 Topline data analysis of the phase 1/2 clinical trial evaluating AOC 1001 in adult patients with myotonic dystrophy type 1: MARINA.
Authors: Johnson, N.1 (AUTHOR), Day, J.2 (AUTHOR), Hamel, J.3 (AUTHOR), Thornton, C.3 (AUTHOR), Subramony, S.4 (AUTHOR), Soltanzadeh, P.5 (AUTHOR), Statland, J.6 (AUTHOR), Wicklund, M.7 (AUTHOR), Arnold, W.8 (AUTHOR), Freimer, M.8 (AUTHOR), DiTrapani, K.9 (AUTHOR), Heusner, C.9 (AUTHOR), Chen, C.9 (AUTHOR), Cho, H.1 (AUTHOR), McEvoy, B.9 (AUTHOR), Zhu, Y.9 (AUTHOR), Tai, L.9 (AUTHOR), Ackermann, E.9 (AUTHOR)
Source: Neuromuscular Disorders. 2023 Supplement 1, Vol. 33, pS69-S69. 1p.
Database: Academic Search Ultimate
Description
ISSN:09608966
DOI:10.1016/j.nmd.2023.07.036