Development of a rigorous approach for retrospective natural history studies in leukodystrophies.
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| Title: | Development of a rigorous approach for retrospective natural history studies in leukodystrophies. |
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| Authors: | Sevagamoorthy, Anjana1 (AUTHOR), Gavazzi, Francesco1 (AUTHOR), Sherbini, Omar1 (AUTHOR), Vincent, Ariel1 (AUTHOR), D'Aiello, Russel1 (AUTHOR), Modesti, Nicholson1 (AUTHOR), Mutua, Sylvia1 (AUTHOR), Yu, Emily1 (AUTHOR), Woidill, Sarah1 (AUTHOR), Schmidt, Johanna L.1 (AUTHOR), Pizzino, Amy1 (AUTHOR), Shults, Justine1 (AUTHOR), Vanderver, Adeline1 (AUTHOR), Adang, Laura A.1 (AUTHOR) |
| Source: | Molecular Genetics & Metabolism. Feb2024, Vol. 141 Issue 2, pN.PAG-N.PAG. 1p. |
| Database: | Academic Search Ultimate |
| ISSN: | 10967192 |
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| DOI: | 10.1016/j.ymgme.2023.108041 |