Development of a rigorous approach for retrospective natural history studies in leukodystrophies.

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Bibliographic Details
Title: Development of a rigorous approach for retrospective natural history studies in leukodystrophies.
Authors: Sevagamoorthy, Anjana1 (AUTHOR), Gavazzi, Francesco1 (AUTHOR), Sherbini, Omar1 (AUTHOR), Vincent, Ariel1 (AUTHOR), D'Aiello, Russel1 (AUTHOR), Modesti, Nicholson1 (AUTHOR), Mutua, Sylvia1 (AUTHOR), Yu, Emily1 (AUTHOR), Woidill, Sarah1 (AUTHOR), Schmidt, Johanna L.1 (AUTHOR), Pizzino, Amy1 (AUTHOR), Shults, Justine1 (AUTHOR), Vanderver, Adeline1 (AUTHOR), Adang, Laura A.1 (AUTHOR)
Source: Molecular Genetics & Metabolism. Feb2024, Vol. 141 Issue 2, pN.PAG-N.PAG. 1p.
Database: Academic Search Ultimate
Description
ISSN:10967192
DOI:10.1016/j.ymgme.2023.108041