Long‐term safety and efficacy outcomes of valoctocogene roxaparvovec gene transfer up to 6 years post‐treatment.

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Bibliographic Details
Title: Long‐term safety and efficacy outcomes of valoctocogene roxaparvovec gene transfer up to 6 years post‐treatment.
Authors: Symington, Emily1 (AUTHOR) emily.symington1@nhs.net, Rangarajan, Savita2 (AUTHOR), Lester, Will3 (AUTHOR), Madan, Bella4 (AUTHOR), Pierce, Glenn F.5 (AUTHOR), Raheja, Priyanka6 (AUTHOR), Robinson, Tara M.7 (AUTHOR), Osmond, Dane7 (AUTHOR), Russell, Chris B.7 (AUTHOR), Vettermann, Christian7 (AUTHOR), Agarwal, Suresh K.7 (AUTHOR), Li, Mingjin7 (AUTHOR), Wong, Wing Yen7 (AUTHOR), Laffan, Michael8 (AUTHOR)
Source: Haemophilia. Mar2024, Vol. 30 Issue 2, p320-330. 11p.
Database: Academic Search Ultimate
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Description
ISSN:13518216
DOI:10.1111/hae.14936