Early spinal muscular atrophy treatment following newborn screening: A 20‐month review of the first Italian regional experience.
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| Title: | Early spinal muscular atrophy treatment following newborn screening: A 20‐month review of the first Italian regional experience. |
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| Authors: | Gagliardi, Delia1 (AUTHOR) delia.gagliardi@unimi.it, Canzio, Eleonora2 (AUTHOR), Orsini, Paola3 (AUTHOR), Conti, Pasquale2 (AUTHOR), Sinisi, Vita2 (AUTHOR), Maggiore, Cosimo2 (AUTHOR), Santarsia, Maria Carla2 (AUTHOR), Lagioia, Giuseppina4 (AUTHOR), Lupis, Giovanna2 (AUTHOR), Roppa, Isabella2 (AUTHOR), Scianatico, Gaetano2 (AUTHOR), Mancini, Daniela2 (AUTHOR), Corti, Stefania1,5 (AUTHOR), Comi, Giacomo Pietro1,6 (AUTHOR), Gentile, Mattia3 (AUTHOR) mattia.gentile@asl.bari.it, Gagliardi, Delio2 (AUTHOR) |
| Source: | Annals of Clinical & Translational Neurology. May2024, Vol. 11 Issue 5, p1090-1096. 7p. |
| Database: | Academic Search Ultimate |
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| ISSN: | 23289503 |
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| DOI: | 10.1002/acn3.52018 |