Evaluation of neuroretina following i.v. or intra‐CSF AAV9 gene replacement in mice with MPS IIIA, a childhood dementia.

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Title: Evaluation of neuroretina following i.v. or intra‐CSF AAV9 gene replacement in mice with MPS IIIA, a childhood dementia.
Authors: Beard, Helen1 (AUTHOR), Winner, Leanne1 (AUTHOR), Shoubridge, Andrew2 (AUTHOR), Parkinson‐Lawrence, Emma3 (AUTHOR), Lau, Adeline A.1 (AUTHOR), Mubarokah, Siti N.1 (AUTHOR), Lance, Tabitha‐Rose1 (AUTHOR), King, Barbara1 (AUTHOR), Scott, William1 (AUTHOR), Snel, Marten F.4 (AUTHOR), Trim, Paul J.4 (AUTHOR), Hemsley, Kim M.1 (AUTHOR) kim.hemsley@flinders.edu.au
Source: CNS Neuroscience & Therapeutics. Aug2024, Vol. 30 Issue 8, p1-13. 13p.
Database: Academic Search Ultimate
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ISSN:17555930
DOI:10.1111/cns.14919