Evaluation of neuroretina following i.v. or intra‐CSF AAV9 gene replacement in mice with MPS IIIA, a childhood dementia.

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Title: Evaluation of neuroretina following i.v. or intra‐CSF AAV9 gene replacement in mice with MPS IIIA, a childhood dementia.
Authors: Beard, Helen1 (AUTHOR), Winner, Leanne1 (AUTHOR), Shoubridge, Andrew2 (AUTHOR), Parkinson‐Lawrence, Emma3 (AUTHOR), Lau, Adeline A.1 (AUTHOR), Mubarokah, Siti N.1 (AUTHOR), Lance, Tabitha‐Rose1 (AUTHOR), King, Barbara1 (AUTHOR), Scott, William1 (AUTHOR), Snel, Marten F.4 (AUTHOR), Trim, Paul J.4 (AUTHOR), Hemsley, Kim M.1 (AUTHOR) kim.hemsley@flinders.edu.au
Source: CNS Neuroscience & Therapeutics. Aug2024, Vol. 30 Issue 8, p1-13. 13p.
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  Data: Evaluation of neuroretina following i.v. or intra‐CSF AAV9 gene replacement in mice with MPS IIIA, a childhood dementia.
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        Value: 10.1111/cns.14919
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              Text: Aug2024
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