Long-term follow-up of givosiran treatment in patients with acute intermittent porphyria from a phase 1/2, 48-month open-label extension study.

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Title: Long-term follow-up of givosiran treatment in patients with acute intermittent porphyria from a phase 1/2, 48-month open-label extension study.
Authors: Sardh, Eliane1 (AUTHOR) eliane.sardh@ki.se, Balwani, Manisha2 (AUTHOR), Rees, David C.3 (AUTHOR), Anderson, Karl E.4 (AUTHOR), Jia, Gang5 (AUTHOR), Sweetser, Marianne T.6 (AUTHOR), Wang, Bruce7 (AUTHOR)
Source: Orphanet Journal of Rare Diseases. 10/3/2024, Vol. 19 Issue 1, p1-14. 14p.
Database: Academic Search Ultimate
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ISSN:17501172
DOI:10.1186/s13023-024-03284-w