14P X-linked myotubular myopathy: 3-year follow-up of a prospective international natural history.
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| Title: | 14P X-linked myotubular myopathy: 3-year follow-up of a prospective international natural history. |
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| Authors: | Seferian, A.1 (AUTHOR), Annoussamy, M.2 (AUTHOR), Fer, F.2 (AUTHOR), Lilien, C.1,3 (AUTHOR), Gidaro, T.1 (AUTHOR), Schara-Schmidt, U.4 (AUTHOR), Braun, F.4,5 (AUTHOR), D'Amico, A.6 (AUTHOR), Daron, A.7 (AUTHOR), González, A. Hernández8 (AUTHOR), de Lattre, C.9,10 (AUTHOR), Villerot, C.11 (AUTHOR), Behin, A.12 (AUTHOR), Arnal, J.13 (AUTHOR), Mayer, M.14 (AUTHOR), Bellance, R.15 (AUTHOR), Davion, J.16 (AUTHOR), Hogrel, J.17 (AUTHOR), Servais, L.1 (AUTHOR) |
| Source: | Neuromuscular Disorders. 2024 Supplement 1, Vol. 43, pN.PAG-N.PAG. 1p. |
| Database: | Academic Search Ultimate |
| ISSN: | 09608966 |
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| DOI: | 10.1016/j.nmd.2024.07.221 |