627P The FORCE(TM) platform achieves robust and durable DUX4 suppression and improves muscle function in facioscapulohumeral muscular dystrophy mouse model.
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| Title: | 627P The FORCE(TM) platform achieves robust and durable DUX4 suppression and improves muscle function in facioscapulohumeral muscular dystrophy mouse model. |
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| Authors: | Picariello, T.1 (AUTHOR), Natoli, T.1 (AUTHOR), Yoder, N.1 (AUTHOR), Yao, M.1 (AUTHOR), Valdivia, B.1 (AUTHOR), Tahaei, E.1 (AUTHOR), Johnson, J.1 (AUTHOR), Qiu, Q.1 (AUTHOR), More, P.1 (AUTHOR), Schlaefke, L.1 (AUTHOR), Yang, S.1 (AUTHOR), Basiri, B.1 (AUTHOR), Weeden, T.1 (AUTHOR), Beskrovnaya, O.1 (AUTHOR), Zanotti, S.1 (AUTHOR) |
| Source: | Neuromuscular Disorders. 2024 Supplement 1, Vol. 43, pN.PAG-N.PAG. 1p. |
| Database: | Academic Search Ultimate |
| ISSN: | 09608966 |
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| DOI: | 10.1016/j.nmd.2024.07.370 |